drugset / Trial / NCT05540860
A Study of EDG-5506 in Children With Duchenne Muscular Dystrophy (LYNX)
RandomizedSequentialQuadruple-blindTreatment
Summary
The LYNX study is a 2-part, multicenter, Phase 2 study of safety, pharmacokinetics and biomarkers in children with Duchenne muscular dystrophy including a randomized, double-blind, placebo-controlled part A, followed by an open-label part B.
Timeline
- Start
- 2022-10-24
- Primary completion
- 2027-01
- Completion
- 2027-01
Drugs
| Evaluation | Drug | Modality | Dose | Route |
|---|---|---|---|---|
| Subject | Sevasemten | Small molecule | — | Oral |