drugset / Trial / NCT05541627

A Study to Evaluate AB-1001 Striatal Administration in Adults With Early Manifest Huntington's Disease

NCT05541627 ↗

Phase 1/2 Active not recruiting 5 enrolled AskBio Inc
Non-randomizedSequentialOpen-labelTreatment

Summary

A Phase I/II Dose-Finding Study to Evaluate Striatal Administration of AB-1001 (previously BV-101) in Adults with Early Manifest Huntington's Disease

Timeline

Start
2022-10-12
Primary completion
2024-04-04
Completion
2028-04

Drugs

EvaluationDrugModalityDoseRoute
Subject AB-1001 Gene therapy (AAV / viral vector) — Other

Indications