drugset / Trial / NCT05561985

Expanded Access Use of Itacitinib to Treat a Single Patient With STAT1 Gain of Function (GOF) Disease

NCT05561985

Expanded access Available Incyte Corporation

Summary

Expanded access use of Itacitinib to treat a single patient with aplastic anemia.

Timeline

Start
Primary completion
Completion

Drugs

EvaluationDrugModalityDoseRoute
Subject Itacitinib Small molecule

Indications

No indication recorded.