drugset / Trial / NCT05573698

Study to Evaluate Multiple Ascending Dose and Multi-Dose of DT-216 in Adult Patients With Friedreich Ataxia

NCT05573698 ↗

Phase 1 Completed 32 enrolled Design Therapeutics, Inc.
RandomizedSequentialQuadruple-blindTreatment

Summary

The purpose of this study is to evaluate the safety, tolerability, pharmacokinetic, and pharmacodynamic effects of multiple doses of intravenous DT-216 in adult patients with Friedrich Ataxia.

Timeline

Start
2022-09-27
Primary completion
2023-08-25
Completion
2023-08-25

Drugs

EvaluationDrugModalityDoseRoute
Subject DT-216 Unknown — Intravenous

Indications