drugset / Trial / NCT05629559
4D-310 in Adults With Fabry Disease and Cardiac Involvement
Non-randomizedSequentialOpen-labelTreatment
Summary
This is a prospective multicenter, open-label, dose-escalation trial to assess the safety, tolerability, and pharmacodynamics of 4D-310 following a single IV administration. The study population is comprised of adult males and females with Fabry Disease and cardiac involvement
Timeline
- Start
- 2022-10-16
- Primary completion
- 2026-06
- Completion
- 2030-06
Drugs
| Evaluation | Drug | Modality | Dose | Route |
|---|---|---|---|---|
| Subject | DUVALGAGENE OTIPARVOVEC | Gene therapy (AAV / viral vector) | — | Intravenous |