drugset / Trial / NCT05765981
An Early Clinical Trial to Evaluate VGN-R09b for Treatment of Aromatic L-amino Acid Decarboxylase (AADC) Deficiency.
Phase 0
Recruiting
6 enrolled
Shanghai Jiao Tong University School of Medicine
Shanghai Vitalgen BioPharma Co., Ltd. · collab
NaSingle-groupOpen-labelTreatment
Summary
This early Phase trial is to prove the safety and efficacy of VGN-R09b to treat patients with AADC deficiency.
Timeline
- Start
- 2023-01-30
- Primary completion
- 2025-02-20
- Completion
- 2029-02-20
Drugs
| Evaluation | Drug | Modality | Dose | Route |
|---|---|---|---|---|
| Subject | VGN-R09b | Gene therapy (AAV / viral vector) | — | Other |