drugset / Trial / NCT05876312

Safety, Tolerability, PK and PD of ADX-038 in Healthy Participants and Paroxysmal Nocturnal Hemoglobinuria (PNH) Patients

NCT05876312

RandomizedParallel-groupTriple-blindTreatment

Summary

The first-in-human Phase 1/Phase 2a study described herein will evaluate the safety, tolerability, pharmacokinetics (PK) and pharmacodynamics (PD) of ADX-038 in both healthy participants (HP) and in patients with paroxysmal nocturnal hemoglobinuria (PNH).

Timeline

Start
2023-08-07
Primary completion
2028-03-31
Completion
2028-07-31

Drugs

EvaluationDrugModalityDoseRoute
Subject QPI-1007 Small interfering RNA (siRNA)