drugset / Trial / NCT06055959

A Study to Evaluate Subcutaneous Zilucoplan in Pediatric Participants With Generalized Myasthenia Gravis

NCT06055959

Phase 2/3 Recruiting 8 enrolled UCB Biopharma SRL
NaSingle-groupOpen-labelTreatment

Summary

The purpose of this study is to assess the pharmacokinetics, pharmacodynamics, safety, tolerability, immunogenicity and activity of zilucoplan (ZLP) in pediatric study participants with generalized myasthenia gravis (gMG).

Timeline

Start
2024-10-16
Primary completion
2026-11-16
Completion
2026-12-25

Drugs

EvaluationDrugModalityDoseRoute
Subject Zilucoplan Peptide Subcutaneous