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drugset / Trial / NCT06153966

PrProfile: A Study to Assess the Safety, Tolerability, Pharmacokinetics and Pharmacodynamics of ION717

NCT06153966 ↗

Phase 1/2 Recruiting 76 enrolled Ionis Pharmaceuticals, Inc.

RandomizedParallel-groupDouble-blindTreatment

Summary

The purpose of this study is to evaluate the safety, tolerability, pharmacokinetics and pharmacodynamics of intrathecal (IT) delivery of ION717.

Timeline

Start: 2024-01-04
Primary completion: 2027-02
Completion: 2030-06

Drugs

Evaluation	Drug	Modality	Dose	Route
Subject	ION717	Unknown	—	Intrathecal

Indications