drugset / Trial / NCT06272149
An Exploratory Clinical Trial of VGN-R08b in Patients With Type II Gaucher Disease
Phase 0
Recruiting
6 enrolled
Xinhua Hospital, Shanghai Jiao Tong University School of Medicine
Shanghai Vitalgen BioPharma Co., Ltd. · collab
NaSingle-groupOpen-labelTreatment
Summary
This exploratory trial is to prove the tolerability and safety of VGN-R08b to treat infants with type II Gaucher disease.
Timeline
- Start
- 2023-03-01
- Primary completion
- 2025-01-15
- Completion
- 2029-02-28
Drugs
| Evaluation | Drug | Modality | Dose | Route |
|---|---|---|---|---|
| Subject | VGN-R08b | Gene therapy (AAV / viral vector) | — | Other |