drugset / Trial / NCT06328608
A Study to Learn About the Safety and Effects of the Study Drug PRX-102 in Children and Adolescents With Fabry Disease
NaSingle-groupOpen-labelTreatment
Summary
A Study to Learn About the Safety and Effects of the Study Drug PRX-102 in Children and Adolescents with Fabry Disease.
Timeline
- Start
- 2025-07-29
- Primary completion
- 2028-10
- Completion
- 2031-04
Drugs
| Evaluation | Drug | Modality | Dose | Route |
|---|---|---|---|---|
| Subject | pegunigalsidase alfa | Protein / enzyme biologic | 1 mg/kg | Intravenous |