drugset / Trial / NCT06545136

Long Term Follow-up Study of Type-1 Gaucher Subjects Post FLT201 Dose (GALILEO-2)

NCT06545136 ↗

Phase 1/2 Active not recruiting 75 enrolled Spur Therapeutics
NaSingle-groupOpen-labelTreatment

Summary

This is a multicenter, long-term, follow-up trial of participants with Gaucher disease type 1 who received FLT201 treatment in a preceding clinical trial. Participants will be followed for 5 years post-treatment.

Timeline

Start
2024-05-13
Primary completion
2029-05
Completion
2029-05

Drugs

EvaluationDrugModalityDoseRoute
Subject FLT201 Gene therapy (AAV / viral vector) — —