drugset / Trial / NCT06585449

A Study to Evaluate ALN-HTT02 in Adult Patients With Huntington's Disease

NCT06585449 ↗

Phase 1 Recruiting 66 enrolled Alnylam Pharmaceuticals
RandomizedParallel-groupTriple-blindTreatment

Summary

The purpose of this study is to evaluate the safety, tolerability, pharmacodynamics (PD) and pharmacokinetics (PK) of single or repeat doses of ALN-HTT02.

Timeline

Start
2024-10-14
Primary completion
2028-07-05
Completion
2028-07-05

Drugs

EvaluationDrugModalityDoseRoute
Subject ALN-HTT02 Unknown — Intrathecal

Indications