drugset / Trial / NCT06817382

A Study to Investigate the Safety and Biodistribution of a Single Intrathecal (IT) Injection of INS1201 in Ambulatory Males With Duchenne Muscular Dystrophy (DMD)

NCT06817382 ↗

Phase 1 Recruiting 12 enrolled Insmed Gene Therapy LLC
Non-randomizedSequentialOpen-labelTreatment

Summary

The primary objective of this study is to evaluate the safety and tolerability of a single dose of INS1201 via IT administration in ambulatory male participants with DMD.

Timeline

Start
2025-07-22
Primary completion
2028-01-31
Completion
2028-03-31

Drugs

EvaluationDrugModalityDoseRoute
Subject INS1201 Unknown — Intrathecal