drugset / Trial / NCT06826612

A Randomized Study of SPK-10001 Gene Therapy in Participants With Huntington's Disease

NCT06826612 ↗

Phase 1/2 Recruiting 53 enrolled Hoffmann-La Roche
RandomizedSequentialQuadruple-blindTreatment

Summary

The main goal of this study is to evaluate the safety, tolerability, and preliminary efficacy of SPK-10001 in participants with Huntington's Disease.

Timeline

Start
2025-02-21
Primary completion
2035-01-12
Completion
2035-01-12

Drugs

EvaluationDrugModalityDoseRoute
Subject SPK-10001 Gene therapy (AAV / viral vector) — Other

Indications