A Study of SRP-9005 in Limb Girdle Muscular Dystrophy Type 2C/R5 Pediatric and Adult Participants

Summary

This is a study of a single systemic dose of SRP-9005 in pediatric and adult participants with limb girdle muscular dystrophy type 2C/R5 (LGMD2C/R5). It is comprised of 2 parts (Part A, Part B) that will assess safety and efficacy.

Timeline

Start

2025-06-30

Primary completion

2030-11-30

Completion

2032-03-30

Outcome

Outcome not reported

Stopped (Business): “Study was Withdrawn per Sponsor decision.”

Drugs

Indications