drugset / Trial / NCT07019922
A Clinical Trial of Elsunersen in Pediatric SCN2A-DEE to Assess Efficacy and Safety
Non-randomizedSequentialOpen-labelTreatment
Summary
A Multi-Center, Single-Arm Clinical Trial to Investigate the Efficacy and Safety of Elsunersen in Pediatric Participants with Early Onset SCN2A Developmental and Epileptic Encephalopathy
Timeline
- Start
- 2025-08-13
- Primary completion
- 2026-06
- Completion
- 2028-12
Drugs
| Evaluation | Drug | Modality | Dose | Route |
|---|---|---|---|---|
| Subject | Elsunersen | Unknown | 0.5 mg | Intrathecal |
| Subject | Elsunersen | Unknown | 1 mg | Intrathecal |