drugset / Trial / NCT07191912

Confirmatory Study of Govorestat in CMT-SORD

NCT07191912 ↗

Phase 3 Withdrawn Applied Therapeutics, Inc.
RandomizedParallel-groupQuadruple-blindTreatment

Summary

This study is designed to assess the long-term efficacy and clinical benefit of AT-007 in patients with CMT-SORD. This randomized, double-blind study will assess the effect of govorestat compared to placebo in patients with CMT-SORD for up to 36 months.

Timeline

Start
2026-05
Primary completion
2028-10
Completion
2029-01

Outcome

Outcome not reported

Stopped (Enrollment): “The study was withdrawn prior to enrollment as the sponsor decided not to proceed with study initiation.”

Drugs

EvaluationDrugModalityDoseRoute
Comparator Govorestat Small molecule 20 mg/kg Oral