drugset / Trial / NCT07191912
Confirmatory Study of Govorestat in CMT-SORD
RandomizedParallel-groupQuadruple-blindTreatment
Summary
This study is designed to assess the long-term efficacy and clinical benefit of AT-007 in patients with CMT-SORD. This randomized, double-blind study will assess the effect of govorestat compared to placebo in patients with CMT-SORD for up to 36 months.
Timeline
- Start
- 2026-05
- Primary completion
- 2028-10
- Completion
- 2029-01
Outcome
Outcome not reported
Stopped (Enrollment): “The study was withdrawn prior to enrollment as the sponsor decided not to proceed with study initiation.”
Drugs
| Evaluation | Drug | Modality | Dose | Route |
|---|---|---|---|---|
| Comparator | Govorestat | Small molecule | 20 mg/kg | Oral |