drugset / Trial / NCT07220603

An Open-Label Extension Study of PGN-EDODM1 in People With Myotonic Dystrophy Type 1 (FREEDOM-OLE)

NCT07220603 ↗

Phase 2 Recruiting 48 enrolled PepGen Inc
NaSingle-groupOpen-labelTreatment

Summary

The purpose of this study is to learn about the long-term safety and tolerability of PGN-EDODM1 in participants with myotonic dystrophy type 1 (DM1) who have completed a prior study with PGN-EDODM1.

Timeline

Start
2025-12-23
Primary completion
2029-01
Completion
2029-01

Drugs

EvaluationDrugModalityDoseRoute
Subject PGN-EDODM1 Unknown — Intravenous