drugset / Trial / NCT07226206
A Gene Therapy Study of SPK-8011QQ in Adults With Severe or Moderately Severe Hemophilia A
NaSingle-groupOpen-labelTreatment
Summary
This study will assess the safety and tolerability of SPK-8011QQ in adult males with moderately severe to severe hemophilia A.
Timeline
- Start
- 2026-07-14
- Primary completion
- 2031-07-31
- Completion
- 2031-07-31
Drugs
| Evaluation | Drug | Modality | Dose | Route |
|---|---|---|---|---|
| Subject | SPK-8011QQ | Unknown | — | Intravenous |