drugset / Trial / NCT07293546
Phase 1/2 Study of FRF-001, an AAV-9 Gene Therapy, in Patients With FOXG1 Syndrome (FS)
NaSingle-groupOpen-labelTreatment
Summary
The goal of this clinical trial is to learn if FRF-001 is a safe, tolerable, and efficacious treatment for children and adults with FOXG1 syndrome.
Timeline
- Start
- 2026-04
- Primary completion
- 2029-03
- Completion
- 2029-07
Drugs
| Evaluation | Drug | Modality | Dose | Route |
|---|---|---|---|---|
| Subject | FRF-001 | Unknown | — | Other |