drugset / Trial / NCT07293546

Phase 1/2 Study of FRF-001, an AAV-9 Gene Therapy, in Patients With FOXG1 Syndrome (FS)

NCT07293546 ↗

Phase 1/2 Not yet recruiting 12 enrolled FOXG1 Research Foundation
NaSingle-groupOpen-labelTreatment

Summary

The goal of this clinical trial is to learn if FRF-001 is a safe, tolerable, and efficacious treatment for children and adults with FOXG1 syndrome.

Timeline

Start
2026-04
Primary completion
2029-03
Completion
2029-07

Drugs

EvaluationDrugModalityDoseRoute
Subject FRF-001 Unknown — Other

Indications