drugset / Trial / NCT07473973

ENERGY 2: Evaluation of the Efficacy and Safety of INZ-701 in Infants With ENPP1 Deficiency

NCT07473973 ↗

Phase 3 Terminated 2 enrolled Inozyme Pharma BioMarin Pharmaceutical · collab
NaSingle-groupOpen-labelTreatment

Summary

The primary purpose of ENERGY 2 (Study INZ701-105) is to assess the efficacy and safety of INZ-701 in infants with ENPP1 Deficiency.

Timeline

Start
2025-03-26
Primary completion
2026-08-31
Completion
2026-08-31

Outcome

Outcome not reported

Stopped: “Following review of the totality of program data, the sponsor decided to discontinue development of INZ701. The decision was not related to safety.”

Drugs

EvaluationDrugModalityDoseRoute
Subject INZ-701 Protein / enzyme biologic — Subcutaneous