drugset / Trial / NCT07487389

Zilganersen Expanded Access Program for Individuals With Alexander Disease

NCT07487389 ↗

Expanded access Available Ionis Pharmaceuticals, Inc.

Summary

The purpose of the expanded access program (EAP) is to provide access to zilganersen for eligible individuals with Alexander disease (AxD).

Timeline

Start
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Primary completion
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Completion
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Drugs

EvaluationDrugModalityDoseRoute
Background zilganersen Unknown — —

Indications