drugset / Trial / NCT07579910
Intracerebroventricular Tralesinidase Alfa in Children With Mucopolysaccharidosis Type IIIB
RandomizedParallel-groupSingle-blindTreatment
Summary
The primary objectives of this study are to evaluate the effects of Tralesinidase Alfa (TA) on cognition
Timeline
- Start
- 2026-12
- Primary completion
- 2033-08
- Completion
- 2033-08
Drugs
| Evaluation | Drug | Modality | Dose | Route |
|---|---|---|---|---|
| Subject | AX 250 | Protein / enzyme biologic | — | Other |