drugset / Trial / NCT07579910

Intracerebroventricular Tralesinidase Alfa in Children With Mucopolysaccharidosis Type IIIB

NCT07579910 ↗

Phase 3 Not yet recruiting 14 enrolled Spruce Biosciences
RandomizedParallel-groupSingle-blindTreatment

Summary

The primary objectives of this study are to evaluate the effects of Tralesinidase Alfa (TA) on cognition

Timeline

Start
2026-12
Primary completion
2033-08
Completion
2033-08

Drugs

EvaluationDrugModalityDoseRoute
Subject AX 250 Protein / enzyme biologic — Other