drugset / Trial / NCT07601425
Harmony-HHT: ATV-1601 in Participants With Hereditary Hemorrhagic Telangiectasia (HHT)
RandomizedParallel-groupQuadruple-blindTreatment
Summary
This is a 2-part study evaluating ATV-1601 in participants with moderate to severe HHT. Part 1 is a randomized, double-blind, placebo-controlled study evaluating 3 dosing regimens of ATV-1601. Patients completing Part 1 may participate in the Part 2 open-label extension to receive ATV-1601.
Timeline
- Start
- 2026-06
- Primary completion
- 2027-12
- Completion
- 2030-03
Drugs
| Evaluation | Drug | Modality | Dose | Route |
|---|---|---|---|---|
| Subject | ATV-1601 | Unknown | 60 mg | Oral |
| Subject | ATV-1601 | Unknown | 100 mg | Oral |