drugset / Trial / NCT07601425

Harmony-HHT: ATV-1601 in Participants With Hereditary Hemorrhagic Telangiectasia (HHT)

NCT07601425

Phase 1/2 Not yet recruiting 100 enrolled Atavistik Bio, Inc
RandomizedParallel-groupQuadruple-blindTreatment

Summary

This is a 2-part study evaluating ATV-1601 in participants with moderate to severe HHT. Part 1 is a randomized, double-blind, placebo-controlled study evaluating 3 dosing regimens of ATV-1601. Patients completing Part 1 may participate in the Part 2 open-label extension to receive ATV-1601.

Timeline

Start
2026-06
Primary completion
2027-12
Completion
2030-03

Drugs

EvaluationDrugModalityDoseRoute
Subject ATV-1601 Unknown 60 mg Oral
Subject ATV-1601 Unknown 100 mg Oral