drugset / Trial / NCT07681713

Long-Term Efficacy Study of Vatiquinone for the Treatment of Friedreich's Ataxia (FA)

NCT07681713 ↗

Phase 3 Not yet recruiting 120 enrolled PTC Therapeutics
NaSingle-groupOpen-labelTreatment

Summary

The purpose of this study is to confirm the treatment effects of vatiquinone on the key measures of FA disease progression.

Timeline

Start
2026-08-15
Primary completion
2029-03-15
Completion
2029-03-15

Drugs

EvaluationDrugModalityDoseRoute
Subject Vatiquinone Small molecule 200 mg Oral
Subject Vatiquinone Small molecule 400 mg Oral

Indications