Drugs / AAV RPE65
last change Dec 2018 re-read 3 minutes ago

AAV RPE65

Gene therapy (AAV / viral vector)

Developed for
Leber congenital amaurosis
Investigated by
MeiraGTx UK II Ltd

Trials 1

201620172018201920202021202220232024202520262027
PhaseRegistry idDatesIndicationSponsorStatusOutcome
Phase 1/2 NCT02781480 Apr 2016 → Dec 2018 Leber congenital amaurosis MeiraGTx UK II Ltd Completed No outcome recorded

Evidence & citations 3 cited values

Every value below carries the sentence it was read from. 1 source stands behind the page.

FieldValueCited text
Known as AAV RPE65 ClinicalTrials.gov intervention name — accepted as the source's own label NCT02781480 ↗
Modality Gene therapy (AAV / viral vector) “AAV2/5 vector” NCT02781480 ↗
Route Other “Subretinal administration of a single low dose of range AAV-RPE65” NCT02781480 ↗