drugset / Trial / NCT02781480
Clinical Trial of Gene Therapy for the Treatment of Leber Congenital Amaurosis (LCA)
Non-randomizedSequentialOpen-labelTreatment
Summary
A clinical trial of AAV2/5 vector for patients with Defects in RPE65
Timeline
- Start
- 2016-04
- Primary completion
- 2018-12
- Completion
- 2018-12
Drugs
| Evaluation | Drug | Modality | Dose | Route |
|---|---|---|---|---|
| Subject | AAV RPE65 | Gene therapy (AAV / viral vector) | — | Other |