Drugs / Cedazuridine
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Cedazuridine

Small molecule targets CDA via inhibition

Developed for
acute myeloid leukemia · myelodysplastic syndrome · chronic myelomonocytic leukemia · myeloproliferative neoplasm, unclassifiable · acquired polycythemia vera · cancer · castration-resistant prostate carcinoma · chronic myeloid leukemia
+16 more · clonal hematopoiesis of indeterminate potential · diffuse large B-cell lymphoma · essential thrombocythemia · Hodgkins lymphoma · leukemia, myeloid, accelerated-phase · malignant mesothelioma · malignant peripheral nerve sheath tumor · melanoma · mixed phenotype acute leukemia · myelodysplastic/myeloproliferative neoplasm · myelofibrosis · neuroendocrine neoplasm · peripheral T-cell lymphoma, not otherwise specified · Philadelphia-positive myelogenous leukemia · primary myelofibrosis · triple-negative breast carcinoma
Investigated by
National Cancer Institute (NCI) · Taiho Oncology, Inc. · Astex Pharmaceuticals, Inc. · M.D. Anderson Cancer Center · National Comprehensive Cancer Network · Advanced Accelerator Applications
+24 more · Break Through Cancer · Columbia University · Forma Therapeutics, Inc. · Genentech, Inc. · Imperial College London · Jacqueline Garcia, MD · Lachelle D. Weeks, MD, PhD · Massachusetts General Hospital · Memorial Sloan Kettering Cancer Center · National Institutes of Health (NIH) · OHSU Knight Cancer Institute · Oregon Health and Science University · Otsuka Pharmaceutical Co., Ltd. · PETHEMA Foundation · Roswell Park Cancer Institute · Sanjay Mohan · Sidney Kimmel Comprehensive Cancer Center at Johns Hopkins · Stand Up To Cancer · Taiho Pharmaceutical Co., Ltd. · Taiho Pharmaceuticals, Inc. · Takeda · University of Colorado, Denver · Vanderbilt-Ingram Cancer Center · Washington University School of Medicine

Regulatory milestones approvals, filings & regulatory actions · 2 recorded

MilestoneJurisdictionBrandIndicationDateSentence it was read from
Approved EU (EMA) Inaqovi 2023-09-15 europa.eu
Approved US (FDA) INQOVI 2020-07-07 fda.gov

Trials 43 · a red edge is where a trial was stopped

PhaseRegistry idDatesIndicationSponsorStatusOutcome
Phase 01 trial
Phase 0 NCT06802146 Feb 2025 → Dec 2026 expected clonal hematopoiesis of indeterminate potential Lachelle D. Weeks, MD, PhD Recruiting No outcome recorded
Phase 119 trials
Phase 1 NCT06802523 Apr 2026 → Dec 2028 acute myeloid leukemia National Cancer Institute (NCI) Suspended No outcome recorded
Phase 1 NCT06484062 Aug 2025 → Jun 2028 expected acute myeloid leukemia, myelodysplastic syndrome National Cancer Institute (NCI) Recruiting No outcome recorded
Phase 1 NCT05673200 Sep 2023 → Feb 2027 female breast carcinoma, triple-negative breast carcinoma National Cancer Institute (NCI) Suspended No outcome recorded
Phase 1 NCT05403450 Feb 2023 → Dec 2024 peripheral T-cell lymphoma, not otherwise specified Taiho Oncology, Inc. Terminated No outcome recorded
Phase 1 NCT04953910 Dec 2022 → Dec 2026 expected acute myeloid leukemia, myelodysplastic syndrome Taiho Oncology, Inc. Recruiting No outcome recorded
Phase 1 NCT05272384 Nov 2022 → Jun 2027 expected Hodgkins lymphoma, diffuse large B-cell lymphoma National Cancer Institute (NCI) Recruiting No outcome recorded
Phase 1 NCT05396859 Oct 2022 → Jun 2024 overdue acute myeloid leukemia OHSU Knight Cancer Institute Active not recruiting No outcome recorded
Phase 1 NCT05178693 Apr 2022 → Jun 2026 overdue neuroendocrine neoplasm Imperial College London Recruiting No outcome recorded
Phase 1 NCT05037500 Jan 2022 → Dec 2024 castration-resistant prostate carcinoma Roswell Park Cancer Institute Terminated No outcome recorded
Phase 1 NCT04953897 Dec 2021 → Dec 2026 expected acute myeloid leukemia, myelodysplastic syndrome Taiho Oncology, Inc. Recruiting No outcome recorded
Phase 1/29 trials
Phase 1/2 NCT05089370 Jun 2022 → Aug 2026 overdue melanoma University of Colorado, Denver Active not recruiting No outcome recorded
Phase 1/2 NCT04742634 May 2022 → Nov 2033 expected myelodysplastic syndrome Washington University School of Medicine Recruiting No outcome recorded
Phase 1/2 NCT04817241 Feb 2022 → Jun 2025 overdue acute myeloid leukemia National Cancer Institute (NCI) Active not recruiting No outcome recorded
Phase 1/2 NCT05010122 Jul 2021 → Jan 2028 expected acute myeloid leukemia, myelodysplastic syndrome M.D. Anderson Cancer Center Recruiting No outcome recorded
Phase 1/2 NCT04774393 May 2021 → Nov 2027 expected acute myeloid leukemia M.D. Anderson Cancer Center Recruiting No outcome recorded
Phase 1/2 NCT04657081 Feb 2021 → Sep 2024 overdue acute myeloid leukemia Taiho Oncology, Inc. Active not recruiting No outcome recorded
Phase 1/2 NCT04013880 Aug 2019 → Mar 2021 acute myeloid leukemia, myelodysplastic syndrome Vanderbilt-Ingram Cancer Center Withdrawn No outcome recorded
Phase 1/2 NCT03502668 Jul 2018 → Jan 2026 myelodysplastic syndrome Taiho Oncology, Inc. Completed No outcome recorded
Phase 1/2 NCT02103478 Oct 2014 → Jun 2018 myelodysplastic syndrome Astex Pharmaceuticals, Inc. Completed No outcome recorded
Phase 213 trials
Phase 2 NCT07437950 Oct 2026 → May 2029 expected acute myeloid leukemia National Cancer Institute (NCI) Not yet recruiting No outcome recorded
Phase 2 NCT07507760 Apr 2026 → Apr 2029 expected acute myeloid leukemia PETHEMA Foundation Not yet recruiting No outcome recorded
Phase 2 NCT06661915 Aug 2025 → Dec 2027 acquired polycythemia vera, essential thrombocythemia, leukemia, myeloid, accelerated-phase, myelodysplastic/myeloproliferative neoplasm +3 National Cancer Institute (NCI) Suspended No outcome recorded
Phase 2 NCT06577441 Jun 2025 → Mar 2027 expected myelodysplastic syndrome National Cancer Institute (NCI) Recruiting No outcome recorded
Phase 2 NCT06351306 Apr 2024 acute myeloid leukemia Columbia University Withdrawn No outcome recorded
Phase 2 NCT05960773 Jan 2024 → Dec 2026 BAP1-related tumor predisposition syndrome, malignant mesothelioma National Cancer Institute (NCI) Suspended No outcome recorded
Phase 2 NCT05835011 Jun → Aug 2023 myelodysplastic syndrome Astex Pharmaceuticals, Inc. Terminated No outcome recorded
Phase 2 NCT05799079 Apr 2023 → Sep 2024 acute myeloid leukemia Sanjay Mohan Terminated No outcome recorded
Phase 2 NCT05007873 Oct 2021 → Oct 2026 expected Philadelphia-positive myelogenous leukemia, chronic myeloid leukemia M.D. Anderson Cancer Center Recruiting No outcome recorded
Phase 2 NCT04985656 Oct 2021 → Jan 2024 myelodysplastic syndrome Takeda Withdrawn No outcome recorded
Phase 2/31 trial
Phase 2/3 NCT04256317 May 2020 → Nov 2027 expected acute myeloid leukemia, chronic myelomonocytic leukemia, myelodysplastic syndrome Taiho Oncology, Inc. Recruiting No outcome recorded
Also used as a comparator or background therapy in 9 trials
PhaseRegistry idDatesIndicationSponsorStatusOutcome
Phase 12 trials
Phase 1 NCT05456269 Background Jul 2022 → Aug 2023 acute myeloid leukemia, chronic myelomonocytic leukemia, myelodysplastic syndrome Racura Oncology Ltd Withdrawn No outcome recorded
Phase 1 NCT03922555 Background Jul 2019 → Jan 2027 expected nervous system cancer Massachusetts General Hospital Recruiting No outcome recorded
Phase 1/24 trials
Phase 1/2 NCT05148234 Background Nov 2022 → Feb 2023 myelodysplastic syndrome National Cancer Institute (NCI) Terminated No outcome recorded
Phase 1/2 NCT04061421 Background Nov 2021 → Aug 2027 expected myelodysplastic/myeloproliferative neoplasm Michael Savona Recruiting No outcome recorded
Phase 1/2 NCT04655755 Background Jan 2021 → Jul 2028 expected chronic myelomonocytic leukemia, myelodysplastic syndrome M.D. Anderson Cancer Center Active not recruiting No outcome recorded
Phase 1/2 NCT02649790 Background Jan 2016 → Aug 2024 acute myeloid leukemia, castration-resistant prostate carcinoma, colorectal cancer, myelodysplastic syndrome +1 Karyopharm Therapeutics Inc Completed No outcome recorded
Phase 22 trials
Phase 2 NCT07148947 Background Mar 2026 → Dec 2028 expected myeloproliferative neoplasm University of Washington Recruiting No outcome recorded
Phase 2 NCT06672146 Background May 2025 → Mar 2027 expected acute myeloid leukemia National Cancer Institute (NCI) Recruiting No outcome recorded
Phase 31 trial
Phase 3 NCT05883956 Comparator Dec 2023 → Dec 2024 overdue acute myeloid leukemia, chronic myelomonocytic leukemia, myelodysplastic syndrome Otsuka Australia Pharmaceutical Pty Ltd Active not recruiting No outcome recorded

Press releases naming this drug 2 releases

DateIssuerRelease
2023-09-19 Otsuka Pharmaceutical Development & Commercialization, Inc. Otsuka and Astex announce that the European Commission has approved INAQOVI (oral decitabine and cedazuridine) for the treatment of adults with newly diagnosed acute myeloid leukaemia ® otsuka.co.jp
2022-08-22 Otsuka Pharmaceutical Development & Commercialization, Inc. European Medicines Agency commences review of oral fixed-dosecombination of decitabine and cedazuridine for the treatment ofadults with acute myeloid leukemia otsuka.co.jp

Evidence & citations 11 cited values

Every value below carries the sentence it was read from. 54 sources stand behind the page.

FieldValueCited text
Known as Cedazuridine “ABNL MARRO 001 (AM-001) is an Open label, phase 1/2 study within the framework of the ABNL-MARRO that will test novel treatment combinations in MDS/MPN. Each Arm of AM-001 will...” NCT04061421
50

“ASTX727 is a combination of two drugs (cedazuridine and decitabine) that have been designed to target cancer cells with a PCR2 mutation and to disrupt the cells' ability to...” NCT04872543

“simultaneous oral administration with the novel CDA inhibitor cedazuridine increases decitabine bioavailability for the treatment of myelodysplastic syndromes.” PMID 30926081 Apr 2019

“All participants will receive ASTX727 orally (cedazuridine 100mg + 35mg decitabine) Days 0-5 prior to receiving Lutathera Day 8 +/- 2days.” NCT05178693

“ASTX727 is an oral drug product composed of a fixed-dose combination of cedazuridine (E7727), a CDA inhibitor, and decitabine.” NCT03813186

“This research study involves the study drug Inqovi, which is a combination of the drugs decitabine and cedazuridine.” NCT04980404

“35 mg decitabine/100 mg cedazuridine taken by mouth once daily on Days 1, 2, 3 of a 28 day cycle.” NCT04742634

“Multiple-dose oral administration of once-daily decitabine (35 mg) and cedazuridine (100 mg)” NCT04953897

“Multiple-dose oral administration of once-daily decitabine (35 mg) and cedazuridine (100 mg)” NCT04953910

“ASTX727 is a combination drug of 35 mg decitabine and 100 mg cedazuridine.” NCT02649790

“ASTX727 is made up of the 2 study drugs cedazuridine and decitabine.” NCT03922555

“Drug: Cedazuridine Tablets for oral administration” NCT04608110

“oral decitabine (LD) + cedazuridine (E7727)” NCT03502668

“oral decitabine 5mg + cedazuridineNCT03906695

“Decitabine and CedazuridineNCT06802146

cedazuridine + decitabine” NCT04155580

NCT05089370

NCT04256317

NCT03613532

NCT04817241

NCT06661915

NCT05883956

NCT07507760

NCT03875287

NCT04657081

NCT05272384

NCT04985656

NCT05673200

NCT05148234

NCT05403450

NCT06802523

NCT04774393

NCT07437950

NCT06672146

NCT04975919

NCT05037500

NCT05010772

NCT06577441

NCT05396859

NCT05799079

NCT04746235

NCT06484062

NCT04655755

NCT05010122

NCT05007873

NCT05456269

NCT07148947

NCT05960773

NCT06351306

NCT05835011

NCT04953923

Known as CED “Decitabine/cedazuridine (DEC/CED) (a nucleoside metabolic inhibitor and cytidine deaminase inhibitor).” NCT06802146
Known as Cedazuridina ChEMBL registry synonym — accepted as the source's own label CHEMBL3237547
Known as cedazuridine (E7727) cedazuridine (E7727)NCT02103478
Known as CEDAZURIDINE COMPONENT OF ASTX-727 ChEMBL registry synonym — accepted as the source's own label CHEMBL3237547
Known as Cedazuridine component of inqovi ChEMBL registry synonym — accepted as the source's own label CHEMBL3237547
Known as E7727 “ABNL MARRO 001 (AM-001) is an Open label, phase 1/2 study within the framework of the ABNL-MARRO that will test novel treatment combinations in MDS/MPN. Each Arm of AM-001 will...” NCT04061421
3

“ASTX727 is an oral drug product composed of a fixed-dose combination of cedazuridine (E7727), a CDA inhibitor, and decitabine.” NCT03813186

“oral decitabine (LD) + cedazuridine (E7727)” NCT03502668

NCT04013880

Action Inhibit “simultaneous oral administration with the novel CDA inhibitor cedazuridine increases decitabine bioavailability” PMID 30926081 Apr 2019
Modality Small molecule CHEMBL3237547
Route Oral “Participants in Part 3 of the study will also have the opportunity to receive venetoclax plus oral decitabine/cedazuridine after transplantation.” NCT03613532
Target CDA “simultaneous oral administration with the novel CDA inhibitor cedazuridine increases decitabine bioavailability” PMID 30926081 Apr 2019