Drugs / gaboxadol
last change Jun 2025 re-read 2 minutes ago

gaboxadol

also known as MK0928 · OV101 · HLX-0206 · LU 02-030 · NSC-759585

Small molecule

Developed for
insomnia · Angelman syndrome · fragile X syndrome · major depressive disorder
Investigated by
H. Lundbeck A/S · Healx AI · Craig Erickson · Healx Limited

Trials 22 · a red edge is where a trial was stopped

PhaseRegistry idDatesIndicationSponsorStatusOutcome
Phase 11 trial
Phase 1 NCT03109756 Apr → Nov 2017 Angelman syndrome, fragile X syndrome Healx AI Completed No outcome recorded
Phase 26 trials
Phase 2 NCT06334419 Jan 2024 → May 2025 fragile X syndrome Craig Erickson Completed No outcome recorded
Phase 2 NCT03697161 Sep 2018 → Feb 2020 fragile X syndrome Healx AI Completed No outcome recorded
Phase 2 NCT02996305 Jan 2016 → Jun 2018 Angelman syndrome Healx AI Completed No outcome recorded
Phase 2 NCT00807248 Nov 2008 → Dec 2009 major depressive disorder H. Lundbeck A/S Completed No outcome recorded
Phase 2 NCT00266357 Nov 2005 → Mar 2007 insomnia H. Lundbeck A/S Terminated No outcome recorded
Phase 2 NCT00266344 Nov 2005 → Oct 2006 insomnia H. Lundbeck A/S Completed No outcome recorded
Phase 315 trials
Phase 3 NCT04106557 Sep 2019 → Nov 2020 Angelman syndrome Healx AI Completed No outcome recorded
Phase 3 NCT03882918 Jan 2019 → Jun 2021 Angelman syndrome Healx AI Terminated No outcome recorded
Phase 3 NCT00420810 Sep 2006 → Mar 2007 insomnia H. Lundbeck A/S Terminated No outcome recorded
Phase 3 NCT00102167 Feb → Dec 2005 insomnia H. Lundbeck A/S Completed No outcome recorded
Phase 3 NCT00103818 Feb 2005 → Oct 2006 insomnia H. Lundbeck A/S Completed No outcome recorded
Phase 3 NCT00102154 Jan 2005 → ? insomnia H. Lundbeck A/S Withdrawn No outcome recorded
Phase 3 NCT00094666 Nov 2004 → Mar 2007 insomnia H. Lundbeck A/S Terminated No outcome recorded
Phase 3 NCT00094627 Nov 2004 → Apr 2006 insomnia H. Lundbeck A/S Completed No outcome recorded
Phase 3 NCT00095043 Oct 2004 → Jun 2006 insomnia H. Lundbeck A/S Completed No outcome recorded
Phase 3 NCT00095069 Oct 2004 → Feb 2007 insomnia H. Lundbeck A/S Completed No outcome recorded
Also used as a comparator or background therapy in 1 trial
PhaseRegistry idDatesIndicationSponsorStatusOutcome
Phase 2 NCT04823052 Comparator May → Oct 2022 fragile X syndrome Healx Limited Withdrawn No outcome recorded

Evidence & citations 9 cited values

Every value below carries the sentence it was read from. 26 sources stand behind the page.

FieldValueCited text
Known as gaboxadol “OBJECTIVE: To evaluate safety and tolerability and exploratory efficacy end points for gaboxadol (OV101) compared with placebo in individuals with Angelman syndrome (AS).” PMID 33443117 Dec 2020
19

“MK0928, gaboxadol / Duration of Treatment: 6 days for treatment periods (2 days/dose)” NCT00266357

Gaboxadol (OV101) is a δ-subunit-selective, extrasynaptic GABAA receptor agonist” PMID 34690787 Oct 2021

“MK0928, gaboxadol / Duration of Treatment: 10 months” NCT00102154

“MK0928, gaboxadol / Duration of Treatment - 6 weeks” NCT00094666

“MK0928, gaboxadol / Duration of Treatment 3 Weeks” NCT00266344

NCT04823052

NCT00103818

NCT00094627

NCT00209924

NCT00209950

NCT00095069

NCT00807248

NCT06334419

NCT00209937

NCT04106557

NCT00209963

NCT00102167

NCT00209846

NCT00095043

Known as HLX-0206 “Gaboxadol (HLX-0206) Capsule” NCT04823052
Known as LU 02-030 ChEMBL registry synonym — accepted as the source's own label CHEMBL312443
Known as MK0928 “A study to evaluate the efficacy, safety and tolerability of MK-0928 in Primary Insomnia.” NCT00266357
7

MK0928, gaboxadol / Duration of Treatment - 1 year” NCT00095069

MK0928, gaboxadol” NCT00095043

NCT00420810

NCT00102154

NCT00266344

NCT00266357

NCT00094666

Known as NSC-759585 ChEMBL registry synonym — accepted as the source's own label CHEMBL312443
Known as OV101 “OBJECTIVE: To evaluate safety and tolerability and exploratory efficacy end points for gaboxadol (OV101) compared with placebo in individuals with Angelman syndrome (AS).” PMID 33443117 Dec 2020
4

OV101 (gaboxadol), oral, provided once daily at bedtime for 12 week duration” NCT04106557

NCT03882918

NCT03697161

NCT03109756

Action Activate “Gaboxadol is a highly selective orthosteric agonist that activates δ-subunit-containing extrasynaptic γ-aminobutyric acid type A (GABAA) receptors.” PMID 33443117 Dec 2020
Modality Small molecule CHEMBL312443
Route Oral “The purpose of the study is to assess the safety and tolerability of oral OV101 (gaboxadol) in adult and adolescent subjects with Angelman syndrome.” NCT02996305