Drugs / Pegargiminase
last change Jul 2026 re-read 2 minutes ago

Pegargiminase

Protein / enzyme biologic

Developed for
hepatocellular carcinoma · acute myeloid leukemia · glioblastoma · non-small cell lung carcinoma · soft tissue sarcoma · malignant pleural mesothelioma · prostate cancer · small cell lung carcinoma
+21 more · uveal melanoma · argininosuccinic aciduria · colorectal cancer · cutaneous melanoma · diffuse glioma, H3 G34 mutant · diffuse midline glioma, H3 K27M-mutant · gastric cancer · glioma · Her2-receptor negative breast cancer · high grade malignant neoplasm · malignant peritoneal mesothelioma · melanoma · mesothelioma · metabolic dysfunction-associated steatohepatitis · metastatic melanoma · non-Hodgkin lymphoma · obesity disorder · pancreatic neoplasm · prediabetes syndrome · sarcomatoid carcinoma · skin cancer
Investigated by
Polaris Group · Washington University School of Medicine · M.D. Anderson Cancer Center · Memorial Sloan Kettering Cancer Center · Chang Gung Memorial Hospital · Ludwig Institute for Cancer Research
+28 more · AstraZeneca · Austin Health · Barts & The London NHS Trust · Bayer · Biohaven Pharmaceuticals, Inc. · Cancer Research UK · Children's Discovery Institute · Duke University · FDA Office of Orphan Products Development · Global Coalition for Adaptive Research · Hoffmann-La Roche · Kazia Therapeutics Limited · Kintara Therapeutics, Inc. · Knoa Pharma LLC · Krankenhaus Nordwest · NYU Langone Health · National Cancer Institute (NCI) · National Cheng-Kung University Hospital · National Institutes of Health (NIH) · National Taiwan University Hospital · Polaris Pharmaceuticals, Inc. · Queen Mary University of London · Sabine Mueller, MD, PhD · Saint-Luc University Hospital · St. Bartholomew's Hospital · UK: Barts Center for Experimental Cancer Medicine (CECM) for Trial Coordination · University of Miami · Vigeo Therapeutics, Inc.

Trials 37 · a red edge is where a trial was stopped

PhaseRegistry idDatesIndicationSponsorStatusOutcome
Phase 113 trials
Phase 1 NCT05813327 Mar 2024 → Apr 2026 overdue soft tissue sarcoma Washington University School of Medicine Active not recruiting No outcome recorded
Phase 1 NCT05001828 Apr 2022 → May 2026 overdue acute myeloid leukemia Polaris Group Active not recruiting No outcome recorded
Phase 1 NCT03922880 Apr 2019 → Jan 2023 uveal melanoma Memorial Sloan Kettering Cancer Center Completed No outcome recorded
Phase 1 NCT03498222 Jun 2018 → Jan 2020 non-small cell lung carcinoma Queen Mary University of London Withdrawn No outcome recorded
Phase 1 NCT03254732 Jul 2017 → May 2019 high grade malignant neoplasm Polaris Group Terminated No outcome recorded
Phase 1 NCT02875093 Jan 2017 → Jul 2019 acute myeloid leukemia Polaris Group Terminated No outcome recorded
Phase 1 NCT02101580 Nov 2014 → May 2017 pancreatic neoplasm Polaris Group Completed No outcome recorded
Phase 1 NCT02101593 Nov 2014 → Feb 2016 hepatocellular carcinoma Polaris Group Completed No outcome recorded
Phase 1 NCT02029690 Apr 2014 → Aug 2018 glioma, hepatocellular carcinoma, malignant peritoneal mesothelioma, malignant pleural mesothelioma +3 Polaris Group Terminated No outcome recorded
Phase 1 NCT01948843 Apr 2014 → Apr 2016 Her2-receptor negative breast cancer Polaris Group Completed No outcome recorded
Phase 1/26 trials
Phase 1/2 NCT07389278 Mar 2026 → Jun 2032 expected diffuse glioma, H3 G34 mutant, diffuse midline glioma, H3 K27M-mutant, glioblastoma Sabine Mueller, MD, PhD Not yet recruiting No outcome recorded
Phase 1/2 NCT06085729 Feb 2024 → Sep 2027 expected prostate cancer M.D. Anderson Cancer Center Recruiting No outcome recorded
Phase 1/2 NCT06006286 Aug → Nov 2023 hepatocellular carcinoma M.D. Anderson Cancer Center Withdrawn No outcome recorded
Phase 1/2 NCT05616624 Apr 2023 → Jul 2026 overdue non-small cell lung carcinoma, small cell lung carcinoma Washington University School of Medicine Active not recruiting No outcome recorded
Phase 1/2 NCT02102022 Nov 2014 → Feb 2020 colorectal cancer, gastric cancer, hepatocellular carcinoma Polaris Group Terminated No outcome recorded
Phase 1/2 NCT00520299 Jul 2007 → Mar 2010 metastatic melanoma, skin cancer Ludwig Institute for Cancer Research Completed No outcome recorded
Phase 213 trials
Phase 2 NCT05829239 Apr 2024 obesity disorder, prediabetes syndrome Washington University School of Medicine Withdrawn No outcome recorded
Phase 2 NCT06034977 Dec 2023 → Jul 2026 overdue hepatocellular carcinoma Chang Gung Memorial Hospital Recruiting No outcome recorded
Phase 2 NCT05842512 Sep 2023 → Dec 2027 expected metabolic dysfunction-associated steatohepatitis Polaris Group Recruiting No outcome recorded
Phase 2 NCT04965714 Apr 2022 → Feb 2023 hepatocellular carcinoma M.D. Anderson Cancer Center Withdrawn No outcome recorded
Phase 2 NCT04587830 Sep 2020 → Feb 2027 expected glioblastoma Polaris Group Active not recruiting No outcome recorded
Phase 2 NCT03449901 May 2018 → Jul 2022 soft tissue sarcoma Washington University School of Medicine Completed No outcome recorded
Phase 2 NCT01910012 Jan 2015 → Sep 2016 acute myeloid leukemia Polaris Group Completed No outcome recorded
Phase 2 NCT02006030 Oct 2014 → Jul 2016 hepatocellular carcinoma Polaris Group Completed No outcome recorded
Phase 2 NCT01910025 Dec 2013 → Aug 2016 non-Hodgkin lymphoma Polaris Group Completed No outcome recorded
Phase 2 NCT01266018 Jan 2011 → Jan 2014 small cell lung carcinoma Ludwig Institute for Cancer Research Terminated No outcome recorded
Phase 2/32 trials
Phase 2/3 NCT03970447 Jul 2019 → Jun 2028 expected glioblastoma Global Coalition for Adaptive Research Recruiting No outcome recorded
Phase 2/3 NCT02709512 Aug 2017 → Aug 2022 mesothelioma Polaris Group Completed No outcome recorded
Phase 33 trials
Phase 3 NCT05712694 Nov 2023 → May 2026 soft tissue sarcoma Polaris Group Terminated No outcome recorded
Phase 3 NCT05317819 Mar 2022 → Sep 2028 expected hepatocellular carcinoma Polaris Group Recruiting No outcome recorded
Phase 3 NCT01287585 Jul 2011 → Jul 2015 hepatocellular carcinoma Polaris Group Completed No outcome recorded

Evidence & citations 13 cited values

Every value below carries the sentence it was read from. 43 sources stand behind the page.

FieldValueCited text
Known as pegargiminase Pegargiminase (ADI-PEG 20; ADI) degrades arginine and potentiates pemetrexed (Pem) cytotoxicity in argininosuccinate synthetase 1 (ASS1)-deficient malignant pleural mesothelioma (MPM).” PMID 34589965 Sep 2020
1

NCT04965714

Known as 0B7PYQ9YRT ChEMBL registry synonym — accepted as the source's own label CHEMBL3137346
Known as ADI “Pegargiminase (ADI-PEG 20; ADI) degrades arginine and potentiates pemetrexed (Pem) cytotoxicity in argininosuccinate synthetase 1 (ASS1)-deficient malignant pleural mesothelioma (MPM).” PMID 34589965 Sep 2020
Known as ADI PEG 20 “This study is measuring the safety of the study drug, ADI-PEG 20, combined with immunotherapy drugs nivolumab and ipilimumab in treating patients with advanced uveal melanoma.” NCT03922880
43

“The role of the arginine-lowering agent pegylated arginine deiminase (ADI-PEG20) has not been evaluated in a randomized and biomarker-driven study among patients with cancer.” PMID 27584578 Jan 2017

“The efficacy of pegylated ADI (ADI-PEG20) in relapsed/refractory/poor-risk acute myeloid leukemia (AML) was evaluated in 43 patients in a prospective, phase II trial” PMID 28900115 Sep 2017

“Arginine-depleting therapy with pegylated arginine deiminase (ADI-PEG20) was reported to have activity in advanced melanoma in early phase I-II trial” PMID 22472884 Apr 2012

“Phase I/II Study of PEGylated Arginine Deiminase (ADI-PEG20) With Carboplatin and Cabazitaxel in Men With Aggressive Variant Prostate Cancers (AVPC)” NCT06085729

“ADI-PEG 20 will be given on an outpatient basis at a dose of 36 mg/m\^2 via intramuscular injection into either the deltoid or gluteal muscle.” NCT05813327

“Pegylated arginine deiminase (ADI-PEG20) monotherapy depletes circulating arginine, thereby selectively inducing tumor cell death.” PMID 33787078 Mar 2021

“Phase I/II study of pegylated arginine deiminase (ADI-PEG 20) in patients with advanced melanoma.” PMID 22864522 Aug 2012

“Phase I/II study of pegylated arginine deiminase (ADI-PEG 20) in patients with advanced melanoma.” PMID 22864522 Aug 2012

“Thus ADI-PEG 20 is an arginine degrading enzyme, ADI, coupled to PEG.” NCT03254732

“Drug: ADI PEG20” NCT05813327

“Drug: ADI PEG20” NCT03254732

NCT06034977

NCT05842512

NCT00450372

NCT03970447

NCT05317819

NCT03922880

NCT01910025

NCT01279967

NCT07389278

NCT02006030

NCT05616624

NCT01528384

NCT01497925

NCT06006286

NCT05712694

NCT05001828

NCT06085729

NCT02102022

NCT04587830

NCT01665183

NCT02875093

NCT02029690

NCT01266018

NCT01287585

NCT01910012

NCT03498222

NCT02709512

NCT02101593

NCT00056992

NCT05829239

NCT02101580

NCT01948843

Known as ADI-PEG ChEMBL registry synonym — accepted as the source's own label CHEMBL3137346
Known as Adi-peg20 arginine deiminase ChEMBL registry synonym — accepted as the source's own label CHEMBL3137346
Known as ADI-SS ChEMBL registry synonym — accepted as the source's own label CHEMBL3137346
Known as Arginine deiminase pegylated “ADI-PEG 20 (Arginine deiminase pegylated)” NCT07389278
Known as Pegargiminasa ChEMBL registry synonym — accepted as the source's own label CHEMBL3137346
Known as pegylated arginine deiminase “This is a study of ADI-PEG 20 (pegylated arginine deiminase), an arginine degrading enzyme versus placebo in patients with hepatocellular carcinoma who have failed prior...” NCT01287585
7

“ADI-PEG20 (PEGylated arginine deiminase) is an arginine catabolizing enzyme preparation that improves insulin sensitivity, mitochondrial respiration, and energy utilization in...” NCT05829239

“The role of the arginine-lowering agent pegylated arginine deiminase (ADI-PEG20) has not been evaluated in a randomized and biomarker-driven study among patients with cancer.” PMID 27584578 Jan 2017

“Arginine-depleting therapy with pegylated arginine deiminase (ADI-PEG20) was reported to have activity in advanced melanoma in early phase I-II trial” PMID 22472884 Apr 2012

“Phase I/II Study of PEGylated Arginine Deiminase (ADI-PEG20) With Carboplatin and Cabazitaxel in Men With Aggressive Variant Prostate Cancers (AVPC)” NCT06085729

Pegylated arginine deiminase (ADI-PEG20) monotherapy depletes circulating arginine, thereby selectively inducing tumor cell death.” PMID 33787078 Mar 2021

“Phase I/II study of pegylated arginine deiminase (ADI-PEG 20) in patients with advanced melanoma.” PMID 22864522 Aug 2012

NCT03449901

Action Inhibit “arginine-lowering agent” PMID 27584578 Jan 2017
Modality Protein / enzyme biologic “Arginine Deiminase (ADI) formulated with polyethylene glycol (PEG)” NCT00450372
Route Other “a once a week injection of 160 IU/m2 of ADI-PEG 20” NCT00056992