Drugs / N-Acetylcysteine Amide
last change Aug 2026 re-read 2 minutes ago

N-Acetylcysteine Amide

also known as NPI-001
Developed for
Usher syndrome · retinitis pigmentosa · cystinosis
Investigated by
Nacuity Pharmaceuticals, Inc. · Foundation Fighting Blindness · Nacuity Pharmaceuticals, PTY LTD

Trials 4 · a red edge is where a trial was stopped

PhaseRegistry idDatesIndicationSponsorStatusOutcome
Phase 1/22 trials
Phase 1/2 NCT05994534 Oct 2023 → Aug 2026 overdue cystinosis Nacuity Pharmaceuticals, Inc. Active not recruiting No outcome recorded
Phase 1/2 NCT04355689 Sep 2020 → Jun 2025 Usher syndrome Nacuity Pharmaceuticals, Inc. Completed No outcome recorded
Phase 32 trials
Phase 3 NCT07290530 Dec 2026 → Jul 2029 expected Usher syndrome, retinitis pigmentosa Nacuity Pharmaceuticals, Inc. Not yet recruiting No outcome recorded
Phase 3 NCT07710196 Aug 2026 → Feb 2029 expected Usher syndrome, retinitis pigmentosa Nacuity Pharmaceuticals, Inc. Not yet recruiting No outcome recorded

Evidence & citations 3 cited values

Every value below carries the sentence it was read from. 4 sources stand behind the page.

FieldValueCited text
Known as N-acetylcysteine amide ClinicalTrials.gov intervention name — accepted as the source's own label NCT07290530
1

NCT05994534

Known as NPI-001 “N-acetylcysteine amide (NPI-001) tablets (250 mg), taken BID” NCT07290530
2

NCT07710196

NCT04355689

Route Oral oral tablet” NCT04355689