drugset / Trial / NCT05994534
PK and PD Study of NPI-001 and Cysteamine Bitartrate
Non-randomizedCrossoverOpen-labelTreatment
Summary
Safety, pharmacokinetics, and pharmacodynamics of NPI-001 oral solution in cystinosis patients compared with cysteamine.
Timeline
- Start
- 2023-10-29
- Primary completion
- 2026-08
- Completion
- 2026-08
Drugs
| Evaluation | Drug | Modality | Dose | Route |
|---|---|---|---|---|
| Comparator | Cysteamine | Unknown | — | — |
| Subject | N-Acetylcysteine Amide | Unknown | — | Oral |