Drugs / deutivacaftor
last change Jul 2026 re-read 2 minutes ago

deutivacaftor

also known as VX-561 · CTP-656
Developed for
cystic fibrosis
Investigated by
Vertex Pharmaceuticals Incorporated · Concert Pharmaceuticals

Regulatory milestones approvals, filings & regulatory actions · 2 recorded

MilestoneJurisdictionBrandIndicationDateSentence it was read from
Approved EU (EMA) Alyftrek 2025-06-30 europa.eu
Approved US (FDA) ALYFTREK 2024-12-20 fda.gov

Trials 12 · a red edge is where a trial was stopped

PhaseRegistry idDatesIndicationSponsorStatusOutcome
Phase 14 trials
Phase 1 NCT06299709 Mar → May 2024 cystic fibrosis Vertex Pharmaceuticals Incorporated Completed No outcome recorded
Phase 1 NCT06154447 Dec 2023 → Jul 2026 overdue cystic fibrosis Vertex Pharmaceuticals Incorporated Active not recruiting No outcome recorded
Phase 1 NCT02680249 Feb → Apr 2016 Concert Pharmaceuticals Completed No outcome recorded
Phase 1 NCT02599792 Nov 2015 → Apr 2016 Concert Pharmaceuticals Completed No outcome recorded
Phase 1/21 trial
Phase 1/2 NCT03227471 Jan 2017 → Mar 2018 cystic fibrosis Vertex Pharmaceuticals Incorporated Completed No outcome recorded
Phase 24 trials
Phase 2 NCT03912233 Apr → Dec 2019 cystic fibrosis Vertex Pharmaceuticals Incorporated Completed No outcome recorded
Phase 2 NCT03911713 Apr 2019 → Aug 2020 cystic fibrosis Vertex Pharmaceuticals Incorporated Completed No outcome recorded
Phase 2 NCT03224351 Aug 2017 → Feb 2018 cystic fibrosis Vertex Pharmaceuticals Incorporated Completed No outcome recorded
Phase 2 NCT02971839 Dec 2016 → Aug 2017 cystic fibrosis Vertex Pharmaceuticals Incorporated Terminated No outcome recorded
Phase 33 trials
Phase 3 NCT05444257 Nov 2022 → Oct 2026 expected cystic fibrosis Vertex Pharmaceuticals Incorporated Active not recruiting No outcome recorded
Phase 3 NCT05422222 Jun 2022 → Jun 2030 expected cystic fibrosis Vertex Pharmaceuticals Incorporated Active not recruiting No outcome recorded
Phase 3 NCT05033080 Sep 2021 → May 2023 cystic fibrosis Vertex Pharmaceuticals Incorporated Completed No outcome recorded

Press releases naming this drug 6 releases

DateIssuerRelease
2025-07-14 Vertex Pharmaceuticals Incorporated Vertex Announces Broad Reimbursement Agreement With NHS England for ALYFTREK® (Deutivacaftor/Tezacaftor/Vanzacaftor) an Innovative Once-Daily CFTR Modulator for the Treatment of Cystic Fibrosis vrtx.com
2025-03-07 Vertex Pharmaceuticals Incorporated Vertex Announces UK MHRA Approval of ALYFTREK® (Deutivacaftor/Tezacaftor/Vanzacaftor), a Once-Daily Next-in-Class CFTR Modulator for the Treatment of Cystic Fibrosis vrtx.com
2024-07-02 Vertex Pharmaceuticals Incorporated Vertex Announces FDA Acceptance of New Drug Application for Vanzacaftor/Tezacaftor/Deutivacaftor, a Next-In-Class Triple Combination Treatment for Cystic Fibrosis vrtx.com
2024-02-05 Vertex Pharmaceuticals Incorporated Vertex Announces Positive Results From Pivotal Trials of Vanzacaftor/Tezacaftor/Deutivacaftor, Next-In-Class Triple Combination Treatment for Cystic Fibrosis vrtx.com
2017-07-25 Vertex Pharmaceuticals Incorporated Vertex and Concert Pharmaceuticals Complete Asset Purchase Agreement for CTP-656 vrtx.com
2017-03-06 Vertex Pharmaceuticals Incorporated Vertex to Acquire CTP-656 from Concert Pharmaceuticals for the Treatment of Cystic Fibrosis vrtx.com

Evidence & citations 4 cited values

Every value below carries the sentence it was read from. 12 sources stand behind the page.

FieldValueCited text
Known as deutivacaftor “BACKGROUND: In phase 2 trials in people with cystic fibrosis aged 18 years and older, vanzacaftor-tezacaftor-deutivacaftor has been shown to be a safe and effective, once-daily...” PMID 39756425 Jan 2025
4

“The purpose of this study is to evaluate the long-term safety, tolerability, and efficacy of VX-121/tezacaftor/deutivacaftor (VX-121/TEZ/D-IVA) in participants with cystic fibrosis.” NCT05444257

“vanzacaftor (20 mg once daily), tezacaftor (100 mg once daily), and deutivacaftor (250 mg once daily) as two fixed-dose combination tablets in the morning” PMID 39756424 Jan 2025

“Vanzacaftor/tezacaftor/deutivacaftorNCT06299709

NCT06154447

Known as CTP-656 ClinicalTrials.gov intervention name — accepted as the source's own label NCT02680249
1

NCT02599792

Known as VX-561 ClinicalTrials.gov intervention name — accepted as the source's own label NCT02971839
4

NCT03912233

NCT03224351

NCT03227471

NCT03911713

Route Oral “CTP-656 solid oral doses” NCT02599792