drugset / Trial / NCT02971839

Study to Evaluate the Safety and Efficacy of CTP-656 in Patients With Cystic Fibrosis With CFTR Gating Mutations

NCT02971839

Phase 2 Terminated 11 enrolled Vertex Pharmaceuticals Incorporated
RandomizedParallel-groupQuadruple-blindTreatment

Summary

This study will evaluate the efficacy and safety of CTP-656 in patients with cystic fibrosis (CF) who have a cystic fibrosis transmembrane conductance regulator (CFTR) gating mutation.

Timeline

Start
2016-12
Primary completion
2017-08
Completion
2017-08

Drugs

EvaluationDrugModalityDoseRoute
Comparator IVA Unknown
Subject deutivacaftor Unknown 20 mg
Subject deutivacaftor Unknown 100 mg
Subject deutivacaftor Unknown 150 mg

Indications