Phase 0 4 trials
Phase 0
NCT06598332
Aug 2025 → May 2028
acute graft versus host disease
Baylor College of Medicine
Withdrawn
No outcome recorded
Stop: Business
Phase 0
NCT04958486
Jul 2021 → Sep 2023
posterior fossa ependymoma
The University of Texas Health Science Center, Houston
Completed
No outcome recorded
Phase 0
NCT04187703
Nov 2020 → Nov 2026 expected
myelodysplastic syndrome , myelodysplastic/myeloproliferative neoplasm
Benjamin Tomlinson
Recruiting
No outcome recorded
Phase 0
NCT02940483
Feb 2017 → Nov 2018
brain cancer
The University of Texas Health Science Center, Houston
Completed
No outcome recorded
Phase 1 5 trials
Phase 1
NCT06377085
Jul 2025 → Dec 2026 expected
cerebral palsy
Shirley Ryan AbilityLab
Enrolling by invitation
No outcome recorded
Phase 1
NCT06466798
Jul 2024 → Jul 2027
central nervous system cancer , ependymoma , medulloblastoma
Jeffrey Treiber
Withdrawn
No outcome recorded
Phase 1
NCT03572530
Feb 2019 → Nov 2020
ependymoma
The University of Texas Health Science Center, Houston
Completed
No outcome recorded
Phase 1
NCT03206021
Aug 2017 → Aug 2022
central nervous system cancer , childhood ependymoma , childhood malignant neoplasm
The Hospital for Sick Children
Completed
No outcome recorded
Phase 1
NCT00996515
Jun 2008 → Jul 2011
high grade malignant neoplasm
New Mexico Cancer Research Alliance
Completed
No outcome recorded
Phase 1/2 6 trials
Phase 1/2
NCT03825367
Nov 2019 → May 2023
childhood acute myeloid leukemia
Therapeutic Advances in Childhood Leukemia Consortium
Unknown
No outcome recorded
Phase 1/2
NCT02829840
Sep 2016 → Sep 2021
acute myeloid leukemia
M.D. Anderson Cancer Center
Withdrawn
No outcome recorded
Phase 1/2
NCT02096042
Apr 2014 → Aug 2016
leukemia
M.D. Anderson Cancer Center
Terminated
No outcome recorded
Stop: Enrollment
Phase 1/2
NCT01202877
Mar 2011 → Jul 2015
leukemia
M.D. Anderson Cancer Center
Completed
No outcome recorded
Phase 1/2
NCT00946647
Dec 2009 → Apr 2019
acute myeloid leukemia , chronic myelomonocytic leukemia , myelodysplastic syndrome
Novartis Pharmaceuticals
Completed
No outcome recorded
Phase 1/2
NCT01038635
Dec 2009 → Nov 2015
leukemia
M.D. Anderson Cancer Center
Completed
No outcome recorded
Phase 2 14 trials · 1 missed
Phase 2
NCT07522801
Sep 2026 → Dec 2029 expected
—
Philippe ROUSSELOT
Not yet recruiting
No outcome recorded
Phase 2
NCT05317000
Mar 2023 → Jun 2028 expected
head and neck squamous cell carcinoma
Barbara Burtness
Recruiting
No outcome recorded
Phase 2
NCT02204020
Apr 2015
acute myeloid leukemia , myelodysplastic syndrome
University of Pittsburgh
Withdrawn
No outcome recorded
Stop: Enrollment
Phase 2
NCT02497404
Feb 2015 → Jun 2020
acute erythroid leukemia , myelodysplastic syndrome
Weill Medical College of Cornell University
Completed
No outcome recorded
Phase 2
NCT02124174
Jan 2012 → Jan 2022
acute myeloid leukemia , myelodysplastic syndrome
Patrick Stiff
Unknown
No outcome recorded
Phase 2
NCT01053806
Aug 2011 → Mar 2014
myelodysplastic syndrome
Tel-Aviv Sourasky Medical Center
Unknown
No outcome recorded
Phase 2
NCT00997243
Nov 2009 → Sep 2010
leukemia , myelodysplastic syndrome
Alison Walker
Terminated
No outcome recorded
Phase 2
NCT00704704
Sep 2008 → Sep 2010
myelodysplastic syndrome
Tel-Aviv Sourasky Medical Center
Unknown
No outcome recorded
Phase 2
NCT00721214
Jul 2008 → Jun 2014
myelodysplastic syndrome
Virginia Commonwealth University
Completed
No outcome recorded
Phase 2
NCT00439673
May 2007 → Jul 2010
myelodysplastic syndrome
GIMEMA Foundation
Completed
No outcome recorded
Phase 2
NCT00413478
Sep 2006 → Nov 2014
B-cell chronic lymphocytic leukemia
M.D. Anderson Cancer Center
Terminated
Missed primary
Stop: Enrollment
Phase 2
NCT00339196
Jul 2006 → Jul 2008
acute myeloid leukemia , myelodysplastic syndrome
Assistance Publique - Hôpitaux de Paris
Completed
No outcome recorded
Phase 2
NCT00326170
Jul 2005 → Jul 2007
acute myeloid leukemia , myelodysplastic syndrome
M.D. Anderson Cancer Center
Completed
No outcome recorded
Phase 2
NCT00005934
Jun 2000 → Jun 2003
beta-thalassemia major
National Institute of Diabetes and Digestive and Kidney Diseases (NIDDK)
Completed
No outcome recorded
Show 4 more trials
Comparator or background therapy 2 trials
Phase 1
NCT03612739 Background
Dec 2018 → May 2019
acute myeloid leukemia , myelodysplastic syndrome
Celyad Oncology SA
Withdrawn
No outcome recorded
Stop: Business
Phase 2
NCT00382590 Comparator
Aug 2005 → Feb 2008
acute myeloid leukemia , myelodysplastic syndrome
M.D. Anderson Cancer Center
Completed
No outcome recorded