Drugs / Cholic Acid

Regulatory milestones approvals, filings & regulatory actions · 2 recorded

MilestoneJurisdictionBrandIndicationDateSentence it was read from
Approved US (FDA) CHOLBAM 2015-03-17 fda.gov
Approved EU (EMA) Orphacol 2013-09-12 europa.eu

Trials 6 · a red edge is where a trial was stopped

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PhaseRegistry idDatesIndicationSponsorStatusOutcome
Phase 1/21 trial
Phase 1/2 NCT03720990 Mar 2021 → Aug 2022 Smith-Lemli-Opitz syndrome University of Nebraska Completed No outcome recorded
Phase 21 trial
Phase 2 NCT00457639 Apr 2006 → Apr 2011 fatty liver disease University of Texas Southwestern Medical Center Completed No outcome recorded
Phase 33 trials
Phase 3 NCT01115582 Apr → Aug 2010 inborn disorder of bile acid synthesis Mirum Pharmaceuticals, Inc. Completed No outcome recorded
Phase 3 NCT01438411 Jan 2010 → Jul 2016 congenital bile acid synthesis defect Mirum Pharmaceuticals, Inc. Completed No outcome recorded
Phase 3 NCT00007020 Jan 1992 → Dec 2009 Zellweger spectrum disorders, adrenoleukodystrophy, cholestasis Mirum Pharmaceuticals, Inc. Completed No outcome recorded
Phase not applicable1 trial
NCT00004442 ? → Apr 1999 Zellweger spectrum disorders, adrenoleukodystrophy, d-bifunctional protein deficiency University of Cincinnati Terminated No outcome recorded

Evidence & citations 10 cited values

Every value below carries the sentence it was read from. 8 sources stand behind the page.

FieldValueCited text
Known as Cholic Acid ClinicalTrials.gov intervention name — accepted as the source's own label NCT00457639
5

NCT00007020

NCT00004442

NCT01438411

NCT01115582

NCT03720990

Known as 3 alpha,7alpha,12 alpha-trihydroxy-5 beta-cholanoic acid “The IUPAC name for cholic acid is 3 alpha,7alpha,12 alpha-trihydroxy-5 beta-cholanoic acid.” NCT01115582
Known as Cholalic acid ChEMBL registry synonym — accepted as the source's own label CHEMBL205596
Known as Cholbam ChEMBL registry synonym — accepted as the source's own label CHEMBL205596
Known as Kolbam ChEMBL registry synonym — accepted as the source's own label CHEMBL205596
Known as NSC-6135 ChEMBL registry synonym — accepted as the source's own label CHEMBL205596
Known as Orphacol ChEMBL registry synonym — accepted as the source's own label CHEMBL205596
Action Activate “a farnesoid X receptor agonist” PMID 23447519 Apr 2013
Modality Small molecule CHEMBL205596
Route Oral oral cholic acid and oral chenodeoxycholic acid on day 1” NCT00004442