Catalyst Pharmaceuticals to Present Firdapse Phase 3 Trial Results at the 61st Annual Meeting of the American Association of Neuromuscular and Electrodiagnostic Medicine

CORAL GABLES, Fla., Oct. 27, 2014 (GLOBE NEWSWIRE) -- Catalyst Pharmaceutical Partners, Inc. (Nasdaq:CPRX) (Catalyst Pharmaceuticals), a biopharmaceutical company focused on developing and commercializing innovative therapies for people with rare debilitating diseases, today announced that safety and efficacy results from its Firdapse™ Phase 3 trial will be presented as part of an Industry Forum at the 61 st Annual Meeting of the American Association of Neuromuscular and Electrodiagnostic Medicine (AANEM) being held at the Savannah, Georgia International Trade and Convention Center, Oct. 29-Nov. 1. The Catalyst-sponsored forum will occur on Friday, Oct, 31 at 12:00 pm EDT and include presentations on the diagnosis and treatment of LEMS and Congenital Myasthenic Syndrome (CMS) by several Firdapse Phase 3 clinical study investigators and the Firdapse Expanded Access Program (EAP) by Catalyst's chief medical officer. Catalyst will also be exhibiting at booth #515 during the AANEM. The presentation materials will be posted at www.catalystpharma.com in the Investors section under Events & Presentations. October 31 st Agenda: "New Advances in the Diagnosis and Treatment of Lambert-Eaton Myasthenic Syndrome (LEMS)" Clinical Features and Pathophysiology of Lambert-Eaton Myasthenic Syndrome (LEMS) and Congenital Myasthenic Syndrome (CMS) Perry Shieh, MD, PhD Associate Professor Director, Neuromuscular Program UCLA Medical Center Electrodiagnosis and Management of LEMS Yuen So, MD, PhD Professor of Neurology Chief, Neurology Clinic Stanford University Medical Center Initial Firdapse ™ Pivotal Phase 3 Study Safety Results Mazen Dimachkie, MD Professor of Neurology University of Kansas Medical Center Initial Firdapse ™ Pivotal Phase 3 Study Efficacy Results Shin J. Oh, MD Distinguished Professor Emeritus University of Alabama at Birmingham Medical Center Serving the LEMS Patient - Firdapse ™ Expanded Access Program Charles Gorodetzky, MD, PhD Chief Medical Officer Catalyst Pharmaceuticals Further information can be found at: http://catalystpharma.com/pdf/CPP14006_Invite_RD27R2_WEB.pdf About Catalyst Pharmaceuticals Catalyst Pharmaceuticals is a biopharmaceutical company focused on developing and commercializing innovative therapies for people with rare debilitating diseases, including Lambert-Eaton Myasthenic Syndrome (LEMS), infantile spasms, and Tourette Syndrome. Catalyst's lead candidate, Firdapse™ for the treatment of LEMS, recently completed testing in a global, multi-center, pivotal Phase 3 trial and announced positive top-line data. Firdapse™ for the treatment of LEMS, has received Breakthrough Therapy and Orphan Drug Designations from the U.S. Food and Drug Administration (FDA). Firdapse™ is the first and only European approved drug for symptomatic treatment in adults with LEMS. Catalyst is also developing a potentially safer and more potent vigabatrin analog (designated CPP-115) to treat infantile spasms, and epilepsy, as well as other neurological conditions associated with reduced GABAergic signaling, like post-traumatic stress disorder and Tourette Syndrome. CPP-115 has been granted U.S. orphan drug designation for the treatment of infantile spasms by the FDA and has been granted E.U. orphan medicinal product designation for the treatment of West Syndrome by the European Commission. Forward-Looking Statements This press release contains forward-looking statements. Forward-looking statements involve known and unknown risks and uncertainties, which may cause Catalyst's actual results in future periods to differ materially from forecasted results. A number of factors, including whether the receipt of breakthrough therapy designation for Firdapse ™ will expedite the development and review of Firdapse ™ by the FDA or the likelihood that the product will be found to be safe and effective, whether an NDA for Firdapse ™ will ever be accepted for filing by the FDA, the timing of any such NDA filing or acceptance, whether Catalyst will be the first company to receive an approval for amifampridine 3,4-DAP, giving it 7-year marketing exclusivity for its product, whether any of Catalyst's product candidates will ever be approved for commercialization or successfully commercialized, and those other factors described in Catalyst's Annual Report on Form 10-K for the fiscal year 2013 and its other filings with the U.S. Securities and Exchange Commission (SEC), could adversely affect Catalyst. Copies of Catalyst's filings with the SEC are available from the SEC, may be found on Catalyst's website or may be obtained upon request from Catalyst. Catalyst does not undertake any obligation to update the information contained herein, which speaks only as of this date. Tags BIOTECHNOLOGY PHARMACEUTICALS Contact Data Investor Contacts Brian Korb The Trout Group LLC (646) 378-2923 [email protected] Media Contacts David Schull Matt Middleman, M.D. Russo Partners (212) 845-4271 (212) 845-4272 [email protected] [email protected] Company Contact Patrick J. McEnany Catalyst Pharmaceutical Partners, Inc. Chief Executive Officer (305) 529-2522 [email protected] Contact close Contact With a Reader Account, it's easy to send email directly to the contact for this release. Sign up today for your free Reader Account! Already have an account? Log in here. GlobeNewswire window.setTimeout(() => { try { autoFitImages('.featuredNewsH', { debug: false }); } catch (error) { console.error('Error in autoFitImages:', error); } }, 100); Recommended Reading June 30, 2026 08:03 ET | Source: Catalyst Pharmaceuticals, Inc. Vamorolone Demonstrates On-Target Glucocorticoid Activity Without the Immunosuppression Characteristic of Traditional Corticosteroids at Clinical Doses CORAL GABLES, Fla., June 30, 2026 (GLOBE NEWSWIRE) -- Catalyst Pharmaceuticals, Inc. ("Catalyst") (Nasdaq: CPRX), a commercial-stage biopharmaceutical company focused on in-licensing, developing,... 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