drugset / Trial / NCT00069550
Independent Studies of Dextromethorphan and of Donepezil Hydrochloride for Rett Syndrome
Phase 3
Unknown
90 enrolled
Eunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD)
RandomizedFactorialOpen-labelTreatment
Summary
Rett syndrome (RTT) is a disorder in which the nervous system does not develop properly. RTT generally affects girls, but there are some boys who have been diagnosed with RTT. Symptoms of RTT include small brain size, poor language skills, repetitive hand movements, and seizures. This study will evaluate the effectiveness of two drugs in treating the symptoms of RTT.
Timeline
- Start
- 2004-09
- Primary completion
- —
- Completion
- 2008-06
Drugs
| Evaluation | Drug | Modality | Dose | Route |
|---|---|---|---|---|
| Subject | Dextromethorphan | Unknown | — | — |
| Subject | Donepezil | Small molecule | — | — |