drugset / Trial / NCT00613561
Early Diagnosis and Stem Cell Transplantation for Severe Immunodeficiency Diseases
Non-randomizedSingle-groupOpen-labelTreatment
Summary
The hypothesis of this study is that children with severe primary immunodeficiencies will benefit from early stem cell transplantation utilizing a reduced intensity conditioning regimen. This regimen is associated with a low risk of complications and will lead to correction of the underlying immunological defects.
Timeline
- Start
- 2007-12
- Primary completion
- 2012-12
- Completion
- 2017-12
Drugs
| Evaluation | Drug | Modality | Dose | Route |
|---|---|---|---|---|
| Subject | ANTILYMPHOCYTE IMMUNOGLOBULIN (HORSE) | Protein / enzyme biologic | — | — |
| Subject | Busulfan | Small molecule | — | — |
| Subject | Fludarabine | Small molecule | — | — |