Phase 0 2 trials
Phase 0
NCT03910452 Background
Oct 2019 → Jun 2034 expected
chronic granulomatous disease
National Institute of Allergy and Infectious Diseases (NIAID)
Active not recruiting
No outcome recorded
Phase 0
NCT00881556 Background
Aug 2009 → Sep 2015
epidermolysis bullosa
Columbia University
Terminated
No outcome recorded
Phase 1 41 trials
Phase 1
NCT07565220 Background
Aug 2026 → Jun 2029 expected
acute lymphoblastic leukemia , acute myeloid leukemia , myelodysplastic syndrome
Sawa Ito, MD
Recruiting
No outcome recorded
Phase 1
NCT06996119 Background
Jun 2026 → May 2027 expected
acute myeloid leukemia , graft versus host disease , myelodysplastic syndrome
City of Hope Medical Center
Recruiting
No outcome recorded
Phase 1
NCT06506461 Background
Mar 2025 → Dec 2029 expected
sickle cell disease
St. Jude Children's Research Hospital
Recruiting
No outcome recorded
Phase 1
NCT06900192 Background
Mar 2025 → Aug 2029 expected
primary progressive multiple sclerosis , secondary progressive multiple sclerosis
Stanford University
Not yet recruiting
No outcome recorded
Phase 1
NCT05569512 Background
Oct 2022 → Oct 2023
acute myeloid leukemia , childhood malignant neoplasm
Malika Kapadia
Terminated
No outcome recorded
Phase 1
NCT05170828 Background
Sep 2022 → Mar 2024
T-lymphoblastic lymphoma , acute biphenotypic leukemia , acute undifferentiated leukemia , myelodysplastic syndrome
Ossium Health, Inc.
Withdrawn
No outcome recorded
Phase 1
NCT06809699 Background
Aug 2022 → Oct 2026 expected
hematologic disorder
He Huang
Recruiting
No outcome recorded
Phase 1
NCT03259503 Background
Sep 2019 → Nov 2025
Hodgkins lymphoma , T-cell non-Hodgkin lymphoma , diffuse large B-cell lymphoma
M.D. Anderson Cancer Center
Completed
No outcome recorded
Phase 1
NCT03613532 Background
Oct 2018 → May 2026 overdue
acute myeloid leukemia , chronic myelomonocytic leukemia , disease related to hematopoietic stem cell transplant , myelodysplastic syndrome +1
Jacqueline Garcia, MD
Active not recruiting
No outcome recorded
Phase 1
NCT03235973 Background
Apr 2018 → Apr 2020
acute lymphoblastic leukemia , acute myeloid leukemia
Institut Paoli-Calmettes
Unknown
No outcome recorded
Phase 1
NCT03240861 Background
Jul 2017 → Oct 2023
high grade malignant neoplasm , sarcoma
Jonsson Comprehensive Cancer Center
Terminated
No outcome recorded
Phase 1
NCT03018223 Background
Jan 2017 → Dec 2018
Hodgkins lymphoma , acute leukemia , chronic myeloid leukemia , chronic myelomonocytic leukemia +4
H. Lee Moffitt Cancer Center and Research Institute
Completed
No outcome recorded
Phase 1
NCT02916979 Background
Sep 2016 → Jun 2019
Waldenstrom macroglobulinemia , lymphoid leukemia , myelodysplastic syndrome , myelofibrosis +2
Dartmouth-Hitchcock Medical Center
Completed
No outcome recorded
Phase 1
NCT02750254 Background
Jun 2016 → May 2017
acute lymphoblastic leukemia , acute myeloid leukemia , myelodysplastic syndrome
Washington University School of Medicine
Terminated
No outcome recorded
Phase 1
NCT02129582 Background
Nov 2014 → Mar 2019
B-cell chronic lymphocytic leukemia , Hodgkins lymphoma , acute myeloid leukemia , chronic myeloid leukemia +3
Case Comprehensive Cancer Center
Completed
No outcome recorded
Phase 1
NCT02130869 Background
Oct 2014 → Dec 2017
lymphoma , neuroblastoma
St. Jude Children's Research Hospital
Completed
No outcome recorded
Phase 1
NCT02083250 Background
Mar 2014 → Nov 2021
acute lymphoblastic leukemia , acute myeloid leukemia , disease related to hematopoietic stem cell transplant , myelodysplastic syndrome
M.D. Anderson Cancer Center
Completed
No outcome recorded
Phase 1
NCT02057770 Background
Feb 2014 → Jan 2018
acute myeloid leukemia
Washington University School of Medicine
Terminated
No outcome recorded
Phase 1
NCT02472392 Comparator
Apr 2013 → Dec 2016
Ewing sarcoma
University of Louisville
Completed
No outcome recorded
Phase 1
NCT01758328 Background
Dec 2012 → Mar 2025
plasma cell myeloma
Memorial Sloan Kettering Cancer Center
Completed
No outcome recorded
Phase 1
NCT01625351 Background
Aug 2012 → Feb 2020
Ewing sarcoma , Wilms tumor , clear cell adenocarcinoma , germ cell tumor +7
St. Jude Children's Research Hospital
Completed
No outcome recorded
Phase 1
NCT01639690 Background
Jul 2012 → Jul 2027 expected
beta-thalassemia major
San Rocco Therapeutics
Active not recruiting
No outcome recorded
Phase 1
NCT01421173 Background
Aug 2011 → Sep 2015
lymphoma
M.D. Anderson Cancer Center
Completed
No outcome recorded
Phase 1
NCT01455506 Background
May 2009 → Dec 2013
acute myeloid leukemia , myelodysplastic syndrome
Hackensack Meridian Health
Completed
No outcome recorded
Phase 1
NCT00513474 Background
Jan 2008 → Feb 2013
graft versus host disease , leukemia , myelodysplastic syndrome , myelodysplastic/myeloproliferative neoplasm +1
Massachusetts General Hospital
Completed
No outcome recorded
Phase 1
NCT00498316 Background
Jul 2007 → Oct 2016
leukemia , myelodysplastic syndrome
M.D. Anderson Cancer Center
Completed
No outcome recorded
Phase 1
NCT00458250 Background
Sep 2006 → Feb 2008
acute lymphoblastic leukemia , acute myeloid leukemia
Tehran University of Medical Sciences
Completed
No outcome recorded
Phase 1
NCT00402558 Background
May 2006 → Apr 2014
leukemia , myelodysplastic syndrome
M.D. Anderson Cancer Center
Completed
No outcome recorded
Phase 1
NCT00245115 Background
Oct 2005 → Dec 2007
leukemia
Sidney Kimmel Comprehensive Cancer Center at Johns Hopkins
Terminated
No outcome recorded
Phase 1
NCT00623077 Background
Aug 2005 → Jul 2012
central nervous system neoplasm , kidney cancer , liver cancer , retinoblastoma +1
Masonic Cancer Center, University of Minnesota
Terminated
No outcome recorded
Phase 1
NCT00112645 Background
Apr 2005 → Apr 2010
childhood malignant neoplasm , neuroblastoma , sarcoma
Milton S. Hershey Medical Center
Completed
No outcome recorded
Phase 1
NCT00152113 Background
Apr 2005 → Dec 2008
sickle cell disease
St. Jude Children's Research Hospital
Completed
No outcome recorded
Phase 1
NCT00092937 Background
Sep 2004 → Apr 2010
chronic granulomatous disease
National Institute of Allergy and Infectious Diseases (NIAID)
Completed
No outcome recorded
Phase 1
NCT00669890 Background
May 2004 → Dec 2012
acute myeloid leukemia , juvenile myelomonocytic leukemia , myelodysplastic syndrome
New York Medical College
Terminated
No outcome recorded
Phase 1
NCT00304018 Background
Oct 2002 → Mar 2009
leukemia , myelodysplastic syndrome , plasma cell neoplasm
University of California, San Francisco
Completed
No outcome recorded
Phase 1
NCT01020539 Background
Sep 2002 → Jul 2011
acute myeloid leukemia , juvenile myelomonocytic leukemia , myelodysplastic syndrome
Columbia University
Completed
No outcome recorded
Phase 1
NCT00006126 Background
Sep 1999 → Apr 2001
breast cancer , cutaneous melanoma , kidney cancer , lung cancer +1
Northwestern University
Withdrawn
No outcome recorded
Phase 1
NCT00003926 Background
Nov 1998 → Aug 2002
central nervous system neoplasm , childhood germ cell tumor , chordoma , kidney cancer +5
Masonic Cancer Center, University of Minnesota
Terminated
No outcome recorded
Phase 1
NCT00705120 Background
Nov 1995 → Jul 2000
osteogenesis imperfecta
St. Jude Children's Research Hospital
Completed
No outcome recorded
Phase 1
NCT00003060 Background
Mar 1995 → Feb 2001
cutaneous melanoma
Louisiana State University Health Sciences Center Shreveport
Terminated
No outcome recorded
Phase 1
NCT00667927 Background
Mar 1991 → Jan 1995
acute myeloid leukemia
St. Jude Children's Research Hospital
Completed
No outcome recorded
Show 36 more trials
Phase 1/2 45 trials
Phase 1/2
NCT04370795 Comparator
Nov 2025
severe combined immunodeficiency
National Institute of Allergy and Infectious Diseases (NIAID)
Withdrawn
No outcome recorded
Phase 1/2
NCT07113743 Background
Sep 2025 → Sep 2028 expected
granulomatous disease, chronic, X-linked
National Institute of Allergy and Infectious Diseases (NIAID)
Enrolling by invitation
No outcome recorded
Phase 1/2
NCT06959771 Background
Jul 2025 → Oct 2027 expected
hyper-IgM syndrome type 1
National Institute of Allergy and Infectious Diseases (NIAID)
Recruiting
No outcome recorded
Phase 1/2
NCT06851767 Background
May 2025 → Dec 2034 expected
T-B+ severe combined immunodeficiency due to gamma chain deficiency
National Institute of Allergy and Infectious Diseases (NIAID)
Enrolling by invitation
No outcome recorded
Phase 1/2
NCT06325709 Background
Apr 2024 → Dec 2032 expected
granulomatous disease, chronic, X-linked
National Institute of Allergy and Infectious Diseases (NIAID)
Recruiting
No outcome recorded
Phase 1/2
NCT05470491 Background
Jan 2023 → Jul 2026 overdue
HIV infectious disease , hematopoietic and lymphoid cell neoplasm
National Cancer Institute (NCI)
Recruiting
No outcome recorded
Phase 1/2
NCT05463133 Background
Jul 2022 → Dec 2032 expected
chronic granulomatous disease
National Institute of Allergy and Infectious Diseases (NIAID)
Recruiting
No outcome recorded
Phase 1/2
NCT04982354 Background
Jul 2022 → Aug 2031
acute myeloid leukemia
Guenther Koehne
Withdrawn
No outcome recorded
Phase 1/2
NCT05327023 Background
May 2022 → Jul 2028 expected
hematopoietic and lymphoid cell neoplasm
National Cancer Institute (NCI)
Recruiting
No outcome recorded
Phase 1/2
NCT05075681 Background
Nov 2021 → Jun 2024
disease related to hematopoietic stem cell transplant
Chinese PLA General Hospital
Unknown
No outcome recorded
Phase 1/2
NCT03597594 Comparator
Sep 2021 → Jul 2027 expected
severe combined immunodeficiency
St. Jude Children's Research Hospital
Active not recruiting
No outcome recorded
Phase 1/2
NCT04690192 Background
Jan 2021 → Dec 2023
large B-cell lymphoma
Institute of Hematology & Blood Diseases Hospital, China
Completed
No outcome recorded
Phase 1/2
NCT04582604 Background
Sep 2020 → Sep 2023
disease related to hematopoietic stem cell transplant
Chinese PLA General Hospital
Unknown
No outcome recorded
Phase 1/2
NCT03983850 Background
Jul 2019 → Nov 2025 overdue
graft versus host disease , hematopoietic and lymphoid cell neoplasm
National Cancer Institute (NCI)
Active not recruiting
No outcome recorded
Phase 1/2
NCT03653247 Background
Mar 2019 → Jul 2025
sickle cell disease
Sangamo Therapeutics
Completed
No outcome recorded
Phase 1/2
NCT03538899 Background
May 2018 → Jun 2038 expected
severe combined immunodeficiency
University of California, San Francisco
Recruiting
No outcome recorded
Phase 1/2
NCT03765632 Background
Jan 2018 → Sep 2021
severe combined immunodeficiency, autosomal recessive, T cell-negative, B cell-negative, NK cell-negative, due to adenosine deaminase deficiency
Great Ormond Street Hospital for Children NHS Foundation Trust
Completed
No outcome recorded
Phase 1/2
NCT03247088 Background
Jul 2017 → Dec 2027 expected
acute myeloid leukemia
M.D. Anderson Cancer Center
Active not recruiting
No outcome recorded
Phase 1/2
NCT02999984 Background
Dec 2016 → Oct 2018
severe combined immunodeficiency, autosomal recessive, T cell-negative, B cell-negative, NK cell-negative, due to adenosine deaminase deficiency
University of California, Los Angeles
Completed
No outcome recorded
Phase 1/2
NCT02799147 Background
Jun 2016 → Nov 2020
acute lymphoblastic leukemia , mixed phenotype acute leukemia
St. Petersburg State Pavlov Medical University
Completed
No outcome recorded
Phase 1/2
NCT02806375 Background
Jan 2016 → Dec 2018
primary myelofibrosis
St. Petersburg State Pavlov Medical University
Completed
No outcome recorded
Phase 1/2
NCT02629120 Comparator
Dec 2015 → Dec 2027 expected
chronic granulomatous disease
National Institute of Allergy and Infectious Diseases (NIAID)
Active not recruiting
No outcome recorded
Phase 1/2
NCT02282904 Background
Oct 2014 → Apr 2019
chronic granulomatous disease
National Institute of Allergy and Infectious Diseases (NIAID)
Terminated
No outcome recorded
Phase 1/2
NCT02098512 Background
Mar 2014 → Dec 2021
Hodgkins lymphoma
New York Medical College
Unknown
No outcome recorded
Phase 1/2
NCT02025881 Background
Sep 2013 → Oct 2020
medulloblastoma
Gustave Roussy, Cancer Campus, Grand Paris
Terminated
No outcome recorded
Phase 1/2
NCT01852071 Background
Aug 2013 → Aug 2018
severe combined immunodeficiency, autosomal recessive, T cell-negative, B cell-negative, NK cell-negative, due to adenosine deaminase deficiency
University of California, Los Angeles
Completed
No outcome recorded
Phase 1/2
NCT01823198 Background
Jun 2013 → May 2022
acute erythroid leukemia , acute megakaryoblastic leukemia , blast phase chronic myelogenous leukemia, BCR-ABL1 positive , chronic myelomonocytic leukemia +2
M.D. Anderson Cancer Center
Completed
No outcome recorded
Phase 1/2
NCT01734850 Background
Apr 2013 → Sep 2017
HIV infectious disease
Calimmune, Inc.
Completed
No outcome recorded
Phase 1/2
NCT01629511 Background
Nov 2012 → Apr 2018
B-cell chronic lymphocytic leukemia , Richter transformation , disease related to hematopoietic stem cell transplant , prolymphocytic leukemia
M.D. Anderson Cancer Center
Terminated
No outcome recorded
Phase 1/2
NCT01380990 Background
Nov 2012 → Dec 2019
severe combined immunodeficiency, autosomal recessive, T cell-negative, B cell-negative, NK cell-negative, due to adenosine deaminase deficiency
Great Ormond Street Hospital for Children NHS Foundation Trust
Completed
No outcome recorded
Phase 1/2
NCT01701986 Background
Oct 2012 → Jun 2024
B-cell non-Hodgkin lymphoma , Hodgkins lymphoma , T-cell non-Hodgkin lymphoma , disease related to hematopoietic stem cell transplant
M.D. Anderson Cancer Center
Completed
No outcome recorded
Phase 1/2
NCT01306019 Background
Sep 2012 → Dec 2032 expected
T-B+ severe combined immunodeficiency due to gamma chain deficiency
National Institute of Allergy and Infectious Diseases (NIAID)
Recruiting
No outcome recorded
Phase 1/2
NCT01860170 Comparator
Apr 2012 → Mar 2016
hematopoietic and lymphoid cell neoplasm
Corewell Health West
Completed
No outcome recorded
Phase 1/2
NCT03315078 Background
Apr 2012 → Dec 2022
combined immunodeficiency, X-linked
National Institute of Allergy and Infectious Diseases (NIAID)
Unknown
No outcome recorded
Phase 1/2
NCT01129544 Background
Apr 2010 → Mar 2023
severe combined immunodeficiency
David Williams
Completed
No outcome recorded
Phase 1/2
NCT00809276 Background
May 2009 → Dec 2011
leukemia , myelodysplastic syndrome , plasma cell myeloma
Sidney Kimmel Comprehensive Cancer Center at Johns Hopkins
Completed
No outcome recorded
Phase 1/2
NCT00840684 Background
Jan 2009 → May 2011
leukemia
Institut Paoli-Calmettes
Completed
No outcome recorded
Phase 1/2
NCT00822770 Background
Jan 2009 → Oct 2012
disease related to hematopoietic stem cell transplant , leukemia
M.D. Anderson Cancer Center
Completed
No outcome recorded
Phase 1/2
NCT00556452 Background
Oct 2007 → Jun 2011
Hodgkins lymphoma , leukemia , myelodysplastic syndrome , non-Hodgkin lymphoma +1
University of Michigan Rogel Cancer Center
Completed
No outcome recorded
Phase 1/2
NCT00555048 Background
Sep 2007 → Oct 2010
graft versus host disease , leukemia , myelodysplastic syndrome , myelodysplastic/myeloproliferative disease
Fred Hutchinson Cancer Center
Terminated
No outcome recorded
Phase 1/2
NCT00054340 Background
Oct 2002 → Sep 2006
graft versus host disease , leukemia , myelodysplastic syndrome , myelodysplastic/myeloproliferative disease +1
Fred Hutchinson Cancer Center
Completed
No outcome recorded
Phase 1/2
NCT00043810 Background
Jul 2002 → Mar 2005
acute myeloid leukemia , myelodysplastic syndrome
M.D. Anderson Cancer Center
Terminated
No outcome recorded
Phase 1/2
NCT00049634 Background
Jan 2002 → Feb 2007
leukemia , myelodysplastic syndrome , myelodysplastic/myeloproliferative disease , myeloproliferative neoplasm
Fred Hutchinson Cancer Center
Completed
No outcome recorded
Phase 1/2
NCT00281983 Background
Jun 2000 → Jul 2010
B-cell chronic lymphocytic leukemia
German CLL Study Group
Completed
No outcome recorded
Phase 1/2
NCT02577094 Background
? → Jan 2017
B-cell acute lymphoblastic leukemia
Nantes University Hospital
Withdrawn
No outcome recorded
Show 40 more trials
Phase 2 140 trials
Phase 2
NCT07562568 Background
Jun 2026 → Jun 2030 expected
acute lymphoblastic leukemia , acute myeloid leukemia , myelodysplastic syndrome
The First Affiliated Hospital of Soochow University
Not yet recruiting
No outcome recorded
Phase 2
NCT07575412 Background
Jun 2026 → Jun 2029 expected
acute lymphoblastic leukemia , acute myeloid leukemia , myelodysplastic syndrome
The First Affiliated Hospital of Soochow University
Not yet recruiting
No outcome recorded
Phase 2
NCT05617625 Background
Jun 2026 → Jun 2033
graft versus host disease , myelodysplastic syndrome
Guenther Koehne
Suspended
No outcome recorded
Phase 2
NCT07566377 Background
Apr 2026 → Apr 2030 expected
Hodgkins lymphoma , acute lymphoblastic leukemia , acute myeloid leukemia , graft versus host disease +1
Memorial Sloan Kettering Cancer Center
Recruiting
No outcome recorded
Phase 2
NCT07441967 Background
Feb 2026 → Dec 2027 expected
hematopoietic and lymphoid system neoplasm
Institute of Hematology & Blood Diseases Hospital, China
Not yet recruiting
No outcome recorded
Show all 140 trials opens the full record — a long page
Phase 2/3 19 trials
Phase 2/3
NCT07052422 Background
Jul 2025 → Dec 2027 expected
myeloid neoplasm
Nanfang Hospital, Southern Medical University
Not yet recruiting
No outcome recorded
Phase 2/3
NCT04123392 Background
Oct 2019 → Sep 2022
myeloid neoplasm
Nanfang Hospital, Southern Medical University
Unknown
No outcome recorded
Phase 2/3
NCT04098653 Background
Sep 2019 → Aug 2022
disease related to hematopoietic stem cell transplant , myeloid neoplasm
Nanfang Hospital, Southern Medical University
Unknown
No outcome recorded
Phase 2/3
NCT03799224 Background
Dec 2018 → Dec 2021
acute leukemia , disease related to hematopoietic stem cell transplant
Peking University People's Hospital
Unknown
No outcome recorded
Phase 2/3
NCT03793517 Background
Sep 2018 → Oct 2023 overdue
acute myeloid leukemia , disease related to hematopoietic stem cell transplant
Peking University People's Hospital
Recruiting
No outcome recorded
Phase 2/3
NCT03596892 Background
Jul 2018 → Jun 2021
disease related to hematopoietic stem cell transplant , mixed phenotype acute leukemia with MLL rearranged
Nanfang Hospital, Southern Medical University
Unknown
No outcome recorded
Phase 2/3
NCT03530085 Background
Jun 2018 → Apr 2021
acute myeloid leukemia , disease related to hematopoietic stem cell transplant
Nanfang Hospital, Southern Medical University
Unknown
No outcome recorded
Phase 2/3
NCT03256071 Background
Sep 2017 → Sep 2020
acute myeloid leukemia , disease related to hematopoietic stem cell transplant
The First Affiliated Hospital of Soochow University
Unknown
No outcome recorded
Phase 2/3
NCT03229616 Background
Jul 2017 → Jun 2020
diffuse large B-cell lymphoma , disease related to hematopoietic stem cell transplant
Nanfang Hospital, Southern Medical University
Unknown
No outcome recorded
Phase 2/3
NCT02744742 Background
Apr 2016 → Sep 2019
disease related to hematopoietic stem cell transplant , myelodysplastic syndrome
Nanfang Hospital, Southern Medical University
Completed
No outcome recorded
Phase 2/3
NCT01015742 Background
Nov 2009 → Dec 2012
acute lymphoblastic leukemia , acute myeloid leukemia , chronic myeloid leukemia
Tehran University of Medical Sciences
Unknown
No outcome recorded
Phase 2/3
NCT01238328 Background
Sep 2009 → Sep 2012
mucopolysaccharidosis
Tehran University of Medical Sciences
Unknown
No outcome recorded
Phase 2/3
NCT01087398 Background
Sep 2009 → Nov 2012
osteopetrosis
Tehran University of Medical Sciences
Unknown
No outcome recorded
Phase 2/3
NCT00775931 Comparator
Aug 2008 → Jun 2013
osteopetrosis
Masonic Cancer Center, University of Minnesota
Completed
No outcome recorded
Phase 2/3
NCT00630565 Background
Jul 2006 → Jul 2022
leukemia
Masonic Cancer Center, University of Minnesota
Terminated
No outcome recorded
Phase 2/3
NCT01019876 Comparator
Sep 2002 → Sep 2021
Fanconi anemia , bone marrow failure syndrome , osteopetrosis , severe combined immunodeficiency
Columbia University
Completed
No outcome recorded
Phase 2/3
NCT00176839 Background
Jun 2000 → Feb 2012
acute lymphoblastic leukemia , acute myeloid leukemia , myelodysplastic syndrome
Masonic Cancer Center, University of Minnesota
Terminated
No outcome recorded
Phase 2/3
NCT00176878 Background
Jun 2000 → Mar 2009
Diamond-Blackfan anemia , Kostmann syndrome , Shwachman-Diamond syndrome
Masonic Cancer Center, University of Minnesota
Completed
No outcome recorded
Phase 2/3
NCT00176904 Background
Jan 1995 → Jun 2010
GM1 gangliosidosis , Gaucher disease , Krabbe disease , Niemann-Pick disease +6
Masonic Cancer Center, University of Minnesota
Completed
No outcome recorded
Show 14 more trials
Phase 3 30 trials
Phase 3
NCT06673459 Comparator
Dec 2024 → Nov 2029 expected
T-cell leukemia
The First Affiliated Hospital of Soochow University
Not yet recruiting
No outcome recorded
Phase 3
NCT06297772 Background
Jun 2024 → Mar 2026 overdue
acute myeloid leukemia
Ruijin Hospital
Not yet recruiting
No outcome recorded
Phase 3
NCT06079879 Comparator
Dec 2023 → Jul 2027 expected
essential thrombocythemia
Merck Sharp & Dohme LLC
Active not recruiting
No outcome recorded
Phase 3
NCT05991908 Comparator
Oct 2023 → Oct 2025 overdue
acute myeloid leukemia , myelodysplastic syndrome
Shanghai Jiao Tong University School of Medicine
Recruiting
No outcome recorded
Phase 3
NCT05907486 Background
Aug 2023 → Aug 2025
thrombotic disease
The First Affiliated Hospital of Soochow University
Unknown
No outcome recorded
Phase 3
NCT05457556 Background
Mar 2023 → Jun 2026 overdue
acute lymphoblastic leukemia , mixed phenotype acute leukemia , myelodysplastic syndrome
Children's Oncology Group
Active not recruiting
No outcome recorded
Phase 3
NCT05674539 Comparator
Feb 2023 → Dec 2025 overdue
acute myeloid leukemia , disease related to hematopoietic stem cell transplant , myelodysplastic syndrome
Union Hospital, Tongji Medical College, Huazhong University of Science and Technology
Enrolling by invitation
No outcome recorded
Phase 3
NCT05477589 Background
Jun 2022 → Dec 2029 expected
acute myeloid leukemia , disease related to hematopoietic stem cell transplant
Vastra Gotaland Region
Recruiting
No outcome recorded
Phase 3
NCT04945096 Background
Jul 2021 → Jul 2025
graft versus host disease
The First Affiliated Hospital of Soochow University
Unknown
No outcome recorded
Phase 3
NCT04547049 Comparator
Sep 2020 → Apr 2026 overdue
leukemia , myelodysplastic syndrome
First Affiliated Hospital of Zhejiang University
Active not recruiting
No outcome recorded
Phase 3
NCT03384225 Background
Aug 2016 → Jul 2022
acute myeloid leukemia , disease related to hematopoietic stem cell transplant
Shanghai General Hospital, Shanghai Jiao Tong University School of Medicine
Unknown
No outcome recorded
Phase 3
NCT03384212 Background
Aug 2016 → Jul 2022
acute myeloid leukemia , disease related to hematopoietic stem cell transplant
Shanghai General Hospital, Shanghai Jiao Tong University School of Medicine
Unknown
No outcome recorded
Phase 3
NCT02531841 Comparator
Jul 2014 → Nov 2017
diffuse large B-cell lymphoma
University Hospital Freiburg
Unknown
No outcome recorded
Phase 3
NCT01916252 Comparator
Sep 2013 → Nov 2016
plasma cell myeloma
PETHEMA Foundation
Completed
No outcome recorded
Phase 3
NCT01366612 Comparator
Jun 2010 → Aug 2020
acute myeloid leukemia , chronic myeloid leukemia , myelodysplastic syndrome
Hackensack Meridian Health
Terminated
No outcome recorded
Phase 3
NCT02063022 Comparator
Jan 2009 → Apr 2022
Ewing sarcoma
Italian Sarcoma Group
Completed
No outcome recorded
Phase 3
NCT00822393 Comparator
Nov 2008 → Jan 2018
acute myeloid leukemia , myelodysplastic syndrome
medac GmbH
Completed
No outcome recorded
Phase 3
NCT01191957 Background
Jan 2008 → Dec 2012
acute myeloid leukemia
Italian Group for Bone Marrow Transplantation
Completed
No outcome recorded
Phase 3
NCT00334672 Background
Mar 2006 → Nov 2010
—
Children's Cancer and Leukaemia Group
Unknown
No outcome recorded
Phase 3
NCT00049517 Background
Dec 2002 → Mar 2009
leukemia
Eastern Cooperative Oncology Group
Completed
No outcome recorded
Phase 3
NCT00774280 Comparator
May 2002 → Nov 2009
leukemia , myelodysplastic syndrome
Cooperative Study Group A for Hematology
Completed
No outcome recorded
Phase 3
NCT00186966 Background
Mar 2002 → Apr 2009
acute myeloid leukemia
Dutch Childhood Oncology Group
Completed
No outcome recorded
Phase 3
NCT01704716 Comparator
Feb 2002 → Sep 2021 overdue
neuroblastoma
St. Anna Children's Cancer Research
Recruiting
No outcome recorded
Phase 3
NCT00004128 Background
Sep 1999 → Jan 2008
leukemia
European Organisation for Research and Treatment of Cancer - EORTC
Unknown
No outcome recorded
Phase 3
NCT00002868 Background
Nov 1997 → Mar 2004
leukemia
Eastern Cooperative Oncology Group
Completed
No outcome recorded
Phase 3
NCT00003414 Background
Oct 1997 → May 2004
graft versus host disease , lymphoma
Sidney Kimmel Comprehensive Cancer Center at Johns Hopkins
Completed
No outcome recorded
Phase 3
NCT00025402 Background
Jul 1997 → ?
leukemia
III. Medizinische Klinik Mannheim
Unknown
No outcome recorded
Phase 3
NCT00002798 Background
Aug 1996 → Sep 2006
acute erythroid leukemia , acute monocytic leukemia , acute myeloblastic leukemia with maturation , acute myeloblastic leukemia without maturation +8
National Cancer Institute (NCI)
Completed
No outcome recorded
Phase 3
NCT00002789 Background
May 1996 → Sep 2001
leukemia
Fred Hutchinson Cancer Center
Completed
No outcome recorded
Phase 3
NCT00002961 Comparator
Oct 1995 → Feb 2001
leukemia
Children's Hospital of Philadelphia
Terminated
No outcome recorded
Show 25 more trials
Phase 4 3 trials
Phase 4
NCT04009525 Background
Jul 2019 → Jul 2023
beta-thalassemia major
First Affiliated Hospital of Guangxi Medical University
Completed
No outcome recorded
Phase 4
NCT03171831 Background
Apr 2017 → Dec 2021
beta-thalassemia major
First Affiliated Hospital of Guangxi Medical University
Unknown
No outcome recorded
Phase 4
NCT02784561 Background
Jul 2016 → Jul 2019
leukemia
Chinese PLA General Hospital
Unknown
No outcome recorded
Phase not applicable 23 trials
—
NCT07563920 Background
Jun 2026 → Jun 2029 expected
acute myeloid leukemia
Shanghai General Hospital, Shanghai Jiao Tong University School of Medicine
Not yet recruiting
No outcome recorded
—
NCT07588360 Background
Oct 2025 → Oct 2028 expected
acute myeloid leukemia , myelodysplastic syndrome
Fujian Medical University Union Hospital
Recruiting
No outcome recorded
—
NCT05667402 Background
Jan 2023 → Dec 2025
central nervous system leukemia , disease related to hematopoietic stem cell transplant
First Affiliated Hospital Xi'an Jiaotong University
Unknown
No outcome recorded
—
NCT02469974 Background
May 2015 → Aug 2016
myelofibrosis
Marina Kremyanskaya
Withdrawn
No outcome recorded
—
NCT01779882 Comparator
Jan 2013 → Jan 2018
lymphoid neoplasm , myeloid leukemia
University Hospital, Basel, Switzerland
Completed
No outcome recorded
—
NCT01666080 Background
Aug 2012 → Jun 2027 expected
hemoglobinopathy , immunodeficiency disease
Masonic Cancer Center, University of Minnesota
Recruiting
No outcome recorded
—
NCT01247701 Background
Nov 2010 → Oct 2019
myeloid neoplasm
Baylor College of Medicine
Completed
No outcome recorded
—
NCT00950846 Background
Sep 2009 → Jul 2020
—
Baylor College of Medicine
Completed
No outcome recorded
—
NCT00478244 Background
Apr 2007 → Aug 2011
epidermolysis bullosa
Masonic Cancer Center, University of Minnesota
Terminated
No outcome recorded
—
NCT00550992 Background
Jan 2006 → Dec 2020
leukemia
Dutch Childhood Oncology Group
Unknown
No outcome recorded
—
NCT00578344 Background
Jul 2005 → Jul 2012
sickle cell-hemoglobin c disease syndrome
Tami D. John
Terminated
No outcome recorded
—
NCT00295997 Background
May 2005 → ?
kidney cancer , leukemia , myelodysplastic syndrome , myelodysplastic/myeloproliferative neoplasm +1
University of California, San Francisco
Unknown
No outcome recorded
—
NCT00093587 Background
Aug 2004 → ?
graft versus host disease , leukemia
Jonsson Comprehensive Cancer Center
Unknown
No outcome recorded
—
NCT00145587 Background
Jul 2004 → Feb 2009
osteopetrosis
St. Jude Children's Research Hospital
Terminated
No outcome recorded
—
NCT00253552 Background
May 2004 → May 2006
graft versus host disease , leukemia , myelodysplastic syndrome , myelodysplastic/myeloproliferative disease +3
OHSU Knight Cancer Institute
Terminated
No outcome recorded
—
NCT00521430 Background
Apr 2004 → May 2008
benign neoplasm , leukemia , myelodysplastic syndrome , plasma cell neoplasm
Asan Medical Center
Completed
No outcome recorded
—
NCT00578292 Background
Feb 2004 → May 2016
thalassemia
Baylor College of Medicine
Terminated
No outcome recorded
—
NCT00176930 Background
Oct 2001 → Dec 2019
Hodgkins lymphoma , acute myeloid leukemia , chronic lymphocytic leukemia/small lymphocytic lymphoma , chronic myeloid leukemia +3
Masonic Cancer Center, University of Minnesota
Terminated
No outcome recorded
—
NCT00005893 Background
Jun 2000 → ?
beta-thalassemia major , neutropenia , pure red-cell aplasia , sickle cell disease
Fairview University Medical Center
Completed
No outcome recorded
—
NCT00006056 Background
Mar 2000 → ?
Chediak-Higashi syndrome , X-linked lymphoproliferative syndrome , graft versus host disease , secondary hemophagocytic lymphohistiocytosis
Fairview University Medical Center
Unknown
No outcome recorded
—
NCT01499147 Comparator
Feb 2000 → May 2013
Hodgkins lymphoma , acquired polycythemia vera , acute myeloid leukemia , aplastic anemia +4
University of Illinois at Chicago
Completed
No outcome recorded
—
NCT00290628 Background
Oct 1999 → Apr 2007
Diamond-Blackfan anemia , Fanconi anemia , graft versus host disease , leukemia +4
Masonic Cancer Center, University of Minnesota
Terminated
No outcome recorded
—
NCT00296023 Background
Jan 1999 → Jun 2007
leukemia , myelodysplastic syndrome , myeloproliferative neoplasm , plasma cell neoplasm
University of California, San Francisco
Completed
No outcome recorded
Show 18 more trials
Phase not stated 1 trial
—
NCT00423826 Background
Jan 2007 → Jan 2015
leukemia , myelodysplastic syndrome , myelofibrosis , plasma cell neoplasm +1
Barbara Ann Karmanos Cancer Institute
No longer available
No outcome recorded