drugset / Trial / NCT00448357

Allogeneic Hematopoietic Cell Transplantation for Patients With Busulfex-based Regimen

NCT00448357

NaSingle-groupOpen-labelTreatment

Summary

RATIONALE: Giving chemotherapy, such as fludarabine and busulfan, before a donor peripheral stem cell transplant helps stop the growth of cancer or abnormal cells. It also helps stop the patient's immune system from rejecting the donor's stem cells. When the healthy stem cells from a donor are infused into the patient they may help the patient's bone marrow make stem cells, red blood cells, white blood cells, and platelets. Sometimes the transplanted cells from a donor can make an immune response against the body's normal cells. Giving a monoclonal antibody, alemtuzumab, before the transplant and tacrolimus after the transplant may stop this from happening. PURPOSE: The phase I portion of this trial identified the maximum tolerated dose of busulfan after treating 40 patients on a dose-escalation scheme. We are now treating an additional 26 patients on the phase II portion of the trial at a Pharmacokinetic (PK)-directed dose of total area under curve (AUC) 6912 micrometer (uM)-min/24 hours. We transitioned to the Phase II portion of the study in October 2009.

Timeline

Start
2005-10
Primary completion
2015-11
Completion
2015-11

Drugs

EvaluationDrugModalityDoseRoute
Subject Busulfan Small molecule
Subject Thymoglobulin Protein / enzyme biologic 0.5 mg/kg
Subject Thymoglobulin Protein / enzyme biologic 2.5 mg/kg
Background Fludarabine Small molecule 30 mg/m2 Intravenous
Background Methotrexate Small molecule 5 mg/m2
Background Tacrolimus Small molecule 0.03 mg/kg Oral
Background therapeutic allogeneic lymphocytes Cell therapy