Phase 1 4 trials
Phase 1
NCT07052370
Sep 2025 → Dec 2028 expected
hematopoietic and lymphoid system neoplasm
St. Jude Children's Research Hospital
Recruiting
No outcome recorded
Phase 1
NCT00545519
Oct 2006 → Mar 2008
refractory plasma cell neoplasm
Washington University School of Medicine
Completed
No outcome recorded
Phase 1
NCT00670410
Nov 2003 → Dec 2010
neuroblastoma
Columbia University
Terminated
No outcome recorded
Stop: Enrollment
Phase 1
NCT00040651
Jul 2002 → Mar 2007
systemic sclerosis
National Institute of Arthritis and Musculoskeletal and Skin Diseases (NIAMS)
Terminated
No outcome recorded
Phase 1/2 4 trials
Phase 1/2
NCT00679536
May 2008 → May 2015
leukemia
Ann & Robert H Lurie Children's Hospital of Chicago
Unknown
No outcome recorded
Phase 1/2
NCT00885833
Feb 2007 → Mar 2012
Wiskott-Aldrich syndrome
The Korean Society of Pediatric Hematology Oncology
Completed
No outcome recorded
Phase 1/2
NCT00409695
Dec 2006 → Aug 2007
acute graft versus host disease
M.D. Anderson Cancer Center
Terminated
No outcome recorded
Stop: Enrollment
Phase 1/2
NCT00887042
Jun 2006 → May 2012
acute myeloid leukemia
The Korean Society of Pediatric Hematology Oncology
Unknown
No outcome recorded
Phase 2 26 trials · 1 met primary · 2 missed
Phase 2
NCT06872333
Nov 2024 → Jun 2030 expected
disease related to hematopoietic stem cell transplant , sickle cell disease
Masonic Cancer Center, University of Minnesota
Recruiting
No outcome recorded
Phase 2
NCT06066255
Mar 2024 → Mar 2026
hematopoietic and lymphoid cell neoplasm
Institut Paoli-Calmettes
Unknown
No outcome recorded
Phase 2
NCT03852407
Feb 2019 → Nov 2033 expected
Hodgkins lymphoma , acute lymphoblastic leukemia , acute myeloid leukemia , chronic myeloid leukemia +2
University of Liege
Recruiting
No outcome recorded
Phase 2
NCT02877082
Sep 2016 → Jul 2017
chronic lymphocytic leukemia/small lymphocytic lymphoma , chronic myeloid leukemia , diffuse large B-cell lymphoma , follicular lymphoma +5
Emory University
Terminated
No outcome recorded
Phase 2
NCT02544113
Dec 2015 → Jun 2018
liver failure
The Cleveland Clinic
Completed
Missed primary
Phase 2
NCT02627573
Jul 2015 → Apr 2019
atypical chronic myeloid leukemia, BCR-ABL1 negative , chronic myeloid leukemia , myelodysplastic syndrome
St. Petersburg State Pavlov Medical University
Terminated
No outcome recorded
Stop: Enrollment
Phase 2
NCT01556347
Jul 2012 → May 2016
—
Providence Health & Services
Terminated
No outcome recorded
Phase 2
NCT01566656
Mar 2012 → Nov 2016
hematopoietic and lymphoid cell neoplasm
Nantes University Hospital
Completed
No outcome recorded
Phase 2
NCT01246206
Nov 2010 → Oct 2013
hematopoietic and lymphoid cell neoplasm
Barbara Ann Karmanos Cancer Institute
Completed
No outcome recorded
Phase 2
NCT01939171
Jun 2010 → Feb 2012
—
Instituto de Investigación Hospital Universitario La Paz
Completed
No outcome recorded
Phase 2
NCT00906204
Mar 2010 → Jul 2014
end stage renal failure , kidney failure
Wright State University
Completed
Met primary
Phase 2
NCT01135537
Nov 2009 → Jan 2014
autosomal genetic disease , cancer , metabolic disease
The Hospital for Sick Children
Terminated
No outcome recorded
Phase 2
NCT00882323
Nov 2008 → Oct 2012
aplastic anemia
The Korean Society of Pediatric Hematology Oncology
Unknown
No outcome recorded
Phase 2
NCT00709592
Jul 2008 → Feb 2014
Hodgkins lymphoma , acute myeloid leukemia , chronic lymphocytic leukemia/small lymphocytic lymphoma , chronic myeloid leukemia +2
Virginia Commonwealth University
Completed
No outcome recorded
Phase 2
NCT00593645
Nov 2007 → Dec 2008
acute myeloid leukemia , myelodysplastic syndrome
Washington University School of Medicine
Terminated
No outcome recorded
Phase 2
NCT00542828
Oct 2007 → May 2009
myelodysplastic syndrome
Genzyme, a Sanofi Company
Terminated
No outcome recorded
Stop: Enrollment
Phase 2
NCT00750126
Apr 2007 → Apr 2009
cancer , hematopoietic and lymphoid cell neoplasm
University Hospital, Clermont-Ferrand
Unknown
No outcome recorded
Phase 2
NCT00506948
Sep 2006 → Oct 2010
leukemia , lymphoma , myelodysplastic syndrome
M.D. Anderson Cancer Center
Terminated
No outcome recorded
Phase 2
NCT00475020
Jan 2006 → Oct 2017
myelofibrosis
M.D. Anderson Cancer Center
Completed
No outcome recorded
Phase 2
NCT00737685
Jan 2006 → Aug 2012
aplastic anemia
The Korean Society of Pediatric Hematology Oncology
Unknown
No outcome recorded
Phase 2
NCT00806598
May 2005 → Jun 2012
aplastic anemia , myelodysplastic syndrome
M.D. Anderson Cancer Center
Completed
No outcome recorded
Phase 2
NCT00117689
Apr 2005 → Dec 2007
liver disorder , transplant rejection
Genzyme, a Sanofi Company
Completed
No outcome recorded
Phase 2
NCT00062712
Jun 2003 → Mar 2007
—
National Institute of Diabetes and Digestive and Kidney Diseases (NIDDK)
Completed
No outcome recorded
Phase 2
NCT00089947
Jun 2003 → Dec 2005
transplant rejection
Genzyme, a Sanofi Company
Completed
No outcome recorded
Phase 2
NCT00006178
Aug 2000 → Dec 2007
kidney failure
National Institute of Diabetes and Digestive and Kidney Diseases (NIDDK)
Completed
No outcome recorded
Phase 2
NCT00235300
May 2000 → Apr 2003
acute transplant rejection
Genzyme, a Sanofi Company
Completed
Missed primary
Show 16 more trials
Phase 2/3 1 trial
Phase 2/3
NCT03793517
Sep 2018 → Oct 2023 overdue
acute myeloid leukemia , disease related to hematopoietic stem cell transplant
Peking University People's Hospital
Recruiting
No outcome recorded
Phase 3 3 trials
Phase 3
NCT01844635
May 2012 → May 2016
acquired aplastic anemia
Nagoya University
Unknown
No outcome recorded
Phase 3
NCT01028092
Mar 2009 → Mar 2014
—
University Hospital, Brest
Completed
No outcome recorded
Phase 3
NCT00275509
Jan 2007 → Jun 2010
chronic renal failure syndrome
Johns Hopkins University
Completed
No outcome recorded
Phase 4 11 trials · 2 met primary · 1 missed
Phase 4
NCT05743400
Sep 2023 → Apr 2025 overdue
thrombotic microangiopathy
Hospices Civils de Lyon
Recruiting
No outcome recorded
Phase 4
NCT03006419
Dec 2016 → Jul 2019
transplant rejection
Coordinación de Investigación en Salud, Mexico
Completed
No outcome recorded
Phase 4
NCT03088280
Jun 2015 → Jan 2018
—
Hospital Geral de Fortaleza
Unknown
No outcome recorded
Phase 4
NCT01856803
Oct 2013 → Jun 2018
graft versus host disease
Peking University People's Hospital
Completed
Met primary
Phase 4
NCT02083991
Jan 2013 → Jan 2017
diabetes mellitus
Vastra Gotaland Region
Completed
No outcome recorded
Phase 4
NCT01354301
May 2011 → Apr 2014
cytomegalovirus infection , transplant rejection
Hospital do Rim e Hipertensão
Completed
Met primary
Phase 4
NCT01149993
Jun 2010 → Jun 2012
—
Georgetown University
Withdrawn
No outcome recorded
Phase 4
NCT00706680
Feb 2008 → Feb 2009
diabetes mellitus , transplant rejection
University Health Network, Toronto
Unknown
No outcome recorded
Phase 4
NCT01172418
Feb 2006 → May 2010
—
University of Miami
Completed
Missed primary
Phase 4
NCT00685061
Nov 2002 → Sep 2004
—
University of Miami
Completed
No outcome recorded
Phase 4
NCT00681343
Sep 2002 → Oct 2006
—
University of Miami
Completed
No outcome recorded
Show 1 more trial
Phase not applicable 7 trials · 1 met primary
—
NCT03821987
Dec 2018 → Dec 2021
aplastic anemia , engraftment syndrome
Peking University People's Hospital
Unknown
No outcome recorded
—
NCT01280617
Oct 2010 → Nov 2013
acute kidney injury
Lahey Clinic
Completed
Met primary
—
NCT00970073
Aug 2009 → Jun 2015
—
The Cleveland Clinic
Completed
No outcome recorded
—
NCT00714480
Jul 2008 → Dec 2009
immunodeficiency disease
Swedish Medical Center
Completed
No outcome recorded
—
NCT00476229
Jun 2006 → May 2009
leukemia , lymphoma
M.D. Anderson Cancer Center
Completed
No outcome recorded
—
NCT00235781
Jan → Feb 2006
—
Washington University School of Medicine
Terminated
No outcome recorded
—
NCT00088543
Mar 2004 → Apr 2006
acute lymphoblastic leukemia , acute myeloid leukemia , graft versus host disease
Genzyme, a Sanofi Company
Completed
No outcome recorded
Comparator or background therapy 59 trials
Phase 1
NCT05298358 Background
Nov 2022 → Nov 2024
systemic sclerosis
Sidney Kimmel Comprehensive Cancer Center at Johns Hopkins
Terminated
No outcome recorded
Stop: Enrollment
Phase 1
NCT02512497 Background
Dec 2017 → Oct 2023
T-cell large granular lymphocyte leukemia , T-cell prolymphocytic leukemia , peripheral T-cell lymphoma, not otherwise specified , primary cutaneous T-cell lymphoma
Ohio State University Comprehensive Cancer Center
Completed
No outcome recorded
Phase 1
NCT02867800 Background
Jul 2016 → Dec 2021
graft versus host disease , sickle cell disease
Monica Bhatia
Completed
No outcome recorded
Phase 1
NCT00402558 Background
May 2006 → Apr 2014
leukemia , myelodysplastic syndrome
M.D. Anderson Cancer Center
Completed
No outcome recorded
Phase 1
NCT00669890 Background
May 2004 → Dec 2012
acute myeloid leukemia , juvenile myelomonocytic leukemia , myelodysplastic syndrome
New York Medical College
Terminated
No outcome recorded
Phase 1
NCT00579709 Background
Jul 2002 → Dec 2006
DiGeorge syndrome
Sumitomo Pharma Switzerland GmbH
Completed
No outcome recorded
Phase 1/2
NCT07607197 Background
Feb 2024 → May 2027 expected
anti-HLA hyperimmunization , end stage renal failure
Hospital Universitari Vall d'Hebron Research Institute
Recruiting
No outcome recorded
Phase 1/2
NCT00303667 Background
Jan 2005 → Mar 2011
acute myeloid leukemia
Masonic Cancer Center, University of Minnesota
Completed
No outcome recorded
Phase 2
NCT06646497 Background
Jan 2025 → Jan 2030 expected
acquired aplastic anemia
Assistance Publique - Hôpitaux de Paris
Recruiting
No outcome recorded
Phase 2
NCT05735717 Background
May 2023 → Nov 2027 expected
CBL-related disorder , acute lymphoblastic leukemia , acute myeloid leukemia , central nervous system leukemia +6
Masonic Cancer Center, University of Minnesota
Recruiting
No outcome recorded
Phase 2
NCT04903054 Background
Jan → Sep 2022
disease related to solid organ transplantation
National Institute of Allergy and Infectious Diseases (NIAID)
Withdrawn
No outcome recorded
Stop: Enrollment
Phase 2
NCT04888741 Comparator
Feb 2021 → Aug 2027 expected
Hodgkins lymphoma , acute lymphoblastic leukemia , acute myeloid leukemia , chronic myeloid leukemia +4
University of Birmingham
Recruiting
No outcome recorded
Phase 2
NCT04046549 Background
Oct 2019 → Jul 2022
transplant rejection
Amgen
Completed
No outcome recorded
Phase 2
NCT03292861 Comparator
Sep 2018 → Mar 2026 overdue
—
Cedars-Sinai Medical Center
Enrolling by invitation
No outcome recorded
Phase 2
NCT03219359 Background
Feb 2018 → Oct 2028 expected
Crohn disease
Aaron Etra
Recruiting
No outcome recorded
Phase 2
NCT02464878 Background
Jan 2017 → Nov 2022
type 1 diabetes mellitus
Massachusetts General Hospital
Completed
No outcome recorded
Phase 2
NCT02833805 Background
Sep 2016 → Jul 2021
aplastic anemia , bone marrow failure syndrome
Sidney Kimmel Comprehensive Cancer Center at Johns Hopkins
Completed
No outcome recorded
Phase 2
NCT02776202 Background
May 2016 → Dec 2019
sickle cell disease
National Guard Health Affairs
Unknown
No outcome recorded
Phase 2
NCT02582775 Background
Mar 2016 → Nov 2022
epidermolysis bullosa
Masonic Cancer Center, University of Minnesota
Completed
No outcome recorded
Phase 2
NCT02137239 Background
Dec 2015 → May 2019
—
Bristol-Myers Squibb
Completed
No outcome recorded
Phase 2
NCT02495077 Background
Nov 2015 → Jul 2021
—
National Institute of Allergy and Infectious Diseases (NIAID)
Completed
Missed primary
Phase 2
NCT02441803 Background
Sep 2015 → Sep 2020
leukemia
M.D. Anderson Cancer Center
Completed
No outcome recorded
Phase 2
NCT02224872 Background
Aug 2014 → Dec 2021
aplastic anemia , bone marrow failure syndrome
Sidney Kimmel Comprehensive Cancer Center at Johns Hopkins
Completed
No outcome recorded
Phase 2
NCT01490723 Background
Jan 2013 → Apr 2019
leukemia , lymphoma
M.D. Anderson Cancer Center
Completed
No outcome recorded
Phase 2
NCT01622556 Background
Jan 2012 → Feb 2014
hematopoietic and lymphoid system neoplasm
University of Virginia
Terminated
No outcome recorded
Phase 2
NCT01392989 Background
Mar 2011 → Jun 2016
anemia , myelodysplastic syndrome , myeloid leukemia , neural tube defect
Everett Meyer
Completed
Missed primary
Phase 2
NCT00990249 Background
Oct 2009 → May 2016
acute lymphoblastic leukemia
M.D. Anderson Cancer Center
Completed
No outcome recorded
Phase 2
NCT00916045 Background
Sep 2009 → Mar 2012
Hodgkins lymphoma , acute myeloid leukemia , chronic lymphocytic leukemia/small lymphocytic lymphoma , myelodysplastic syndrome
King's College Hospital NHS Trust
Terminated
No outcome recorded
Stop: Enrollment
Phase 2
NCT00899431 Comparator
May 2009 → Oct 2018
B-cell chronic lymphocytic leukemia
M.D. Anderson Cancer Center
Terminated
No outcome recorded
Phase 2
NCT00857389 Background
Mar 2009 → Mar 2019
disease related to hematopoietic stem cell transplant , leukemia , lymphoma
M.D. Anderson Cancer Center
Completed
No outcome recorded
Phase 2
NCT00813124 Background
Dec 2008 → Sep 2014
disease related to hematopoietic stem cell transplant , leukemia
M.D. Anderson Cancer Center
Completed
No outcome recorded
Phase 2
NCT00523809 Background
Aug 2007 → Oct 2011
breast cancer , ovarian cancer
M.D. Anderson Cancer Center
Terminated
No outcome recorded
Stop: Enrollment
Phase 2
NCT00455013 Background
Jul 2007 → Oct 2008
disease related to solid organ transplantation
Bristol-Myers Squibb
Completed
No outcome recorded
Phase 2
NCT00469014 Background
Sep 2006 → Mar 2013
acute myeloid leukemia , chronic myeloid leukemia , myelodysplastic syndrome
M.D. Anderson Cancer Center
Completed
No outcome recorded
Phase 2
NCT00506129 Background
Sep 2003 → Jun 2015
disease related to hematopoietic stem cell transplant , lymphoma
M.D. Anderson Cancer Center
Completed
No outcome recorded
Phase 2/3
NCT03799224 Background
Dec 2018 → Dec 2021
acute leukemia , disease related to hematopoietic stem cell transplant
Peking University People's Hospital
Unknown
No outcome recorded
Phase 2/3
NCT01087398 Background
Sep 2009 → Nov 2012
osteopetrosis
Tehran University of Medical Sciences
Unknown
No outcome recorded
Phase 3
NCT06083129 Comparator
Nov 2023 → Nov 2028 expected
graft versus host disease
Assistance Publique - Hôpitaux de Paris
Recruiting
No outcome recorded
Phase 3
NCT04302805 Comparator
Jul 2020 → Apr 2024
—
Institute for Clinical and Experimental Medicine
Completed
No outcome recorded
Phase 3
NCT01471444 Background
Nov 2011 → Dec 2020
disease related to hematopoietic stem cell transplant , leukemia
M.D. Anderson Cancer Center
Completed
No outcome recorded
Phase 3
NCT01157949 Comparator
Nov 2010 → Nov 2013
—
Cedars-Sinai Medical Center
Withdrawn
No outcome recorded
Phase 3
NCT00592306 Comparator
Jan 2006 → Sep 2009
—
University of California, Los Angeles
Withdrawn
No outcome recorded
Stop: Enrollment
Phase 3
NCT00682292 Comparator
May 2001 → Nov 2006
—
University Hospital, Lille
Completed
No outcome recorded
Phase 4
NCT07203664 Background
Oct 2025 → Dec 2026 expected
—
Hospital Universitario La Paz
Not yet recruiting
No outcome recorded
Phase 4
NCT04009525 Background
Jul 2019 → Jul 2023
beta-thalassemia major
First Affiliated Hospital of Guangxi Medical University
Completed
No outcome recorded
Phase 4
NCT03470961 Comparator
Mar 2018 → Mar 2021
diabetes mellitus , end stage renal failure
Tianjin First Central Hospital
Unknown
No outcome recorded
Phase 4
NCT03171831 Background
Apr 2017 → Dec 2021
beta-thalassemia major
First Affiliated Hospital of Guangxi Medical University
Unknown
No outcome recorded
Phase 4
NCT02745717 Background
Jan 2016 → Dec 2021
aplastic anemia
Shanghai General Hospital, Shanghai Jiao Tong University School of Medicine
Completed
No outcome recorded
Phase 4
NCT02447822 Comparator
Jun 2015 → May 2018
kidney failure
Asan Medical Center
Unknown
No outcome recorded
Phase 4
NCT02130817 Background
Sep 2014 → Oct 2015
end stage renal failure , transplant rejection
University of Wisconsin, Madison
Withdrawn
No outcome recorded
Stop: Enrollment
Phase 4
NCT02683291 Background
Jan 2014 → Jan 2015
cytomegalovirus infection , disease related to solid organ transplantation
Associação Médico Espírita de Botucatu
Completed
No outcome recorded
Phase 4
NCT01895049 Comparator
Aug 2013 → Mar 2016
cytomegalovirus infection
Helio Tedesco Silva Junior
Completed
Met primary
Phase 4
NCT02084446 Background
Dec 2012 → Jul 2014
cytomegalovirus infection , disease related to solid organ transplantation
Ronaldo de Matos Esmeraldo, MD
Completed
No outcome recorded
Phase 4
NCT01312064 Comparator
Apr 2011 → Apr 2012
impaired renal function disease
National Taiwan University Hospital
Terminated
No outcome recorded
Phase 4
NCT00771745 Comparator
Sep 2008 → Jun 2010
transplant rejection
University of Cincinnati
Completed
No outcome recorded
Phase 4
NCT01195194 Background
Mar 2008 → Jun 2012
disease related to solid organ transplantation
Josep M Grinyo
Completed
No outcome recorded
Phase 4
NCT01046955 Comparator
Nov 2005 → Apr 2007
end stage renal failure
University of Miami
Completed
No outcome recorded
—
NCT01850108 Background
May 2013 → Nov 2023
sickle cell disease
Vanderbilt-Ingram Cancer Center
Unknown
No outcome recorded
—
NCT00709293 Comparator
Jul 2008 → May 2009
ischemic disease
University of California, Los Angeles
Withdrawn
No outcome recorded
Stop: Business
Show 54 more trials