drugset / Trial / NCT03799224

Decitabine Plus mBU/CY Preconditioning for Relapse/Refractory Acute Leukemia

NCT03799224

Phase 2/3 Unknown 55 enrolled Peking University People's Hospital
Non-randomizedSingle-groupOpen-labelTreatment

Summary

Allogeneic haematopoietic stem cell transplantation (allo-HSCT) remains one of the currently available curative therapies for acute leukemia (AL). Leukemia relapse is one of the mainly causes of transplant failure. We reported previously that patients with relapse or refractory AL were at very high risk of relapse post allo-HSCT, with cumulative relapse rate of 50-80%. Decitabine has been demonstrated efficacy in the treatment of patients with recurrent or refractory leukemia and myelodysplastic syndrome. It was reported that the combination of decitabine, with busulfan and cyclophosphamide as a preparative regimen for allo-HSCT using HLA-matching donors was safe and effective. In this prospective, single-arm clinical trial, we aimed to examine the efficacy of combining decitabine with modified busulfan and cyclophosphamide (mBU/CY) as a preparative regimen for allo-HSCT in recurrent and refractory AL patients.

Timeline

Start
2018-12-01
Primary completion
2021-12-31
Completion
2023-12-31

Drugs

EvaluationDrugModalityDoseRoute
Subject Decitabine Small molecule 200 mg/m2 Intravenous
Background Busulfan Small molecule 3.2 mg/kg Intravenous
Background Cyclophosphamide Other / unclassified 1.8 g Intravenous
Background Cytarabine Small molecule 2 g Intravenous
Background Cytarabine Small molecule 4 g Intravenous
Background Hydroxyurea Other / unclassified 80 mg/kg Oral
Background Semustine Small molecule 250 mg/m2 Oral
Background Thymoglobulin Protein / enzyme biologic 2.5 mg/kg Intravenous