Triheptanoin Treatment Trial for Patients With Long-chain Fatty Acid Beta-oxidation Defects

Summary

The purpose of this study is to determine if administration Triheptanoin is an effective treatment for defects of the long-chain fatty acid beta-oxidation in young adults or adults. Period of treatment and follow-up will be 16 months.

Timeline

Start

2009-11

Primary completion

2010-03

Completion

2011-10

Outcome

Outcome not reported

Stopped: “IMP management difficulties”

Drugs

Indications