drugset / Trial / NCT02350816
An Extension Study to Determine Safety and Efficacy for Pediatric Patients With MPS Type IIIA Disease Who Participated in Study HGT-SAN-093.
RandomizedParallel-groupOpen-labelTreatment
Summary
This extension study will allow participants to continue receiving treatment with HGT-1410 and to initiate treatment in patients who received no-treatment in Study HGT-SAN-093, and will evaluate the long-term safety and efficacy of the study drug.
Timeline
- Start
- 2015-04-08
- Primary completion
- 2019-04-12
- Completion
- 2019-04-12
Outcome
Outcome not reported
Stopped: “Completion of follow-up period”
Drugs
| Evaluation | Drug | Modality | Dose | Route |
|---|---|---|---|---|
| Comparator | N-SULFOGLUCOSAMINE SULFOHYDROLASE RECOMBINANT | Protein / enzyme biologic | 45 mg | Intrathecal |