drugset / Trial / NCT02599961

Study to Assess the Long Term Safety and Efficacy of UX007 in Participants With Glucose Type 1 Deficiency Syndrome (Glut1 DS)

NCT02599961

Phase 2 Terminated 15 enrolled Ultragenyx Pharmaceutical Inc
NaSingle-groupOpen-labelTreatment

Summary

The primary objective of the study is to evaluate the long-term safety of UX007 in Glut1 DS participants.

Timeline

Start
2015-09-10
Primary completion
2019-10-22
Completion
2019-10-22

Drugs

EvaluationDrugModalityDoseRoute
Subject Triheptanoin Other / unclassified 35 % Oral