drugset / Trial / NCT02960217

Crossover Study to Assess the Efficacy and Safety of UX007 in the Treatment of Movement Disorders Associated With Glucose Transporter Type 1 Deficiency Syndrome (Glut1 DS)

NCT02960217

Phase 3 Terminated 44 enrolled Ultragenyx Pharmaceutical Inc
RandomizedCrossoverQuadruple-blindTreatment

Summary

The primary objective of the study was to evaluate the efficacy and safety of UX007 in the treatment of disabling paroxysmal movement disorders associated with Glut1 DS.

Timeline

Start
2017-04-19
Primary completion
2019-10-09
Completion
2019-10-09

Drugs

EvaluationDrugModalityDoseRoute
Subject Triheptanoin Other / unclassified 130 g Oral