drugset / Trial / NCT03235973

Cladribine Dose Escalation in Conditioning Regimen Prior to Allo-HSCT for Refractory Acute Leukemia and Myelodysplastic Syndromes

NCT03235973

Phase 1 Unknown 29 enrolled Institut Paoli-Calmettes
NaSingle-groupOpen-labelTreatment

Summary

The investigators focused on patients with refractory acute leukemia or MDS and designed a phase 1 trial of escalated cladribine doses in the Cla-Flu-Bu RTC regimen using PK-guided myeloablative busulfan doses. This scheme allows combining different optimization of RTC experienced over years (Flu-Bu RTC, PK-guided myeloablative busulfan doses, a second purine analog cladribine) to approach a specific platform to treat refractory diseases.

Timeline

Start
2018-04-28
Primary completion
2020-04
Completion
2021-04

Drugs

EvaluationDrugModalityDoseRoute
Subject Cladribine Small molecule 10 mg/m2
Subject Cladribine Small molecule 15 mg/m2
Subject Cladribine Small molecule 20 mg/m2
Subject Cladribine Small molecule 25 mg/m2
Background Busulfan Small molecule 100 mg/m2 Intravenous
Background Busulfan Small molecule 130 mg/m2 Intravenous
Background Fludarabine Small molecule 10 mg/m2