drugset / Trial / NCT03599960

Summary

Patients with suspected BPDCN and meeting eligibility criteria will be enrolled in the study. First, BPDCN diagnosis will be confirmed by anatomic pathology (Dr Petrella T, Montreal) and cytologic plus immunophenotyping analysis (Pr Garnache Ottou F, UMR1098 BESANCON). Patients will then receive three 21 days cycles of a combination of chemotherapy (Ida/Metho/L-asp/Dex), followed by an evaluation. Patients with complete response (CR) or complete response with incomplete bone marrow recovery (CRi) will undergo an allo- or auto-SCT and those who are not eligible to the transplantation will have successive 28 days cycles of chemotherapy (Metho/L-asp/Dex). Patients who did not respond to the treatment will be treated by physicians. All patients will be followed for 24 months.

Timeline

Start
2019-05-02
Primary completion
2023-02-13
Completion
2024-11

Drugs

EvaluationDrugModalityDoseRoute
Subject Asparaginase Erwinia chrysanthemi Protein / enzyme biologic 25000 unknown Intravenous
Subject Dexamethasone Small molecule 20 mg Oral
Subject Dexamethasone Small molecule 40 mg Oral
Subject Idarubicin Small molecule 12 mg/m2 Intravenous
Subject Methotrexate Small molecule 500 mg/m2 Intravenous
Subject Methotrexate Small molecule 1000 mg/m2 Intravenous
Subject Methotrexate Small molecule 3000 mg/m2 Intravenous
Subject asparaginase Protein / enzyme biologic 5000 unknown Intravenous
Background Leucovorin Small molecule